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Anti-VEGF Therapy for Acute Thyroid Eye Disease

Phase 2
Recruiting
Conditions
Thyroid Eye Disease
Interventions
Registration Number
NCT04311606
Lead Sponsor
Massachusetts Eye and Ear Infirmary
Brief Summary

The primary objective of this clinical trial is to assess the safety and tolerability of sub-tenon aflibercept in combination with either saline or hyaluronidase (HA) in patients with acute Thyroid Eye Disease (TED) as assessed by the incidence and severity of adverse events from baseline to day 45.

Participants will undergo clinical examinations and receive three injections of aflibercept with saline, aflibercept with hyaluronidase, or hyaluronidase.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
24
Inclusion Criteria
  1. Minimum of 18 years-old
  2. Active Thyroid Eye Disease
  3. Clinical Activity Score (CAS) between 3 and 5, inclusive
  4. Phakic and pseudophakic eyes are allowed in the study.
  5. Willing and able to provide written informed consent after the nature of the study has been explained, and prior to any research-related procedures
  6. Willing and able to comply with clinic visits and study-related procedures
  7. Only one eye will be enrolled. The worse eye (demonstrating any of these features:

worse HVF results, worse restricted motility, worse visual acuity, worse edema, worse proptosis, worse eyelid retraction) will be enrolled. If both eyes are equivalent, we will enroll the non-dominant eye.

Exclusion Criteria
  1. History of orbital, strabismus, or eyelid surgery or orbital radiation
  2. Optic neuropathy or other vision-threatening signs
  3. Patients currently on systemic or topical steroids. If they received steroids in the past, they would require a 6 week washout period and the cumulative dose of steroids must be less than 1 gram of methylprednisolone (or equivalent). During the washout period we will contact patients by phone weekly to monitor their safety and address any concerns they may have related to no longer taking steroids .
  4. Patients who have taken teprotumumab (Tepezza.)
  5. Patients who have received intraocular anti-VEGF medications within 1 year of screening
  6. Patients who have a history of receiving systemic anti-VEGF
  7. Presence of other retinal vascular diseases (diabetic retinopathy, vein occlusion) that could affect the VEGF levels within the eye
  8. History of stroke or prior myocardial infarction
  9. Known hypersensitivity to aflibercept
  10. Infectious conjunctivitis, keratitis, or endophthalmitis of either eye
  11. Presence of a glaucoma shunting or filtration device that is subconjunctival
  12. Previous participation in any studies of investigational drugs within 1 month preceding Day 0
  13. Any clinically significant acute or chronic medical condition that would preclude participation in a clinical study
  14. Pregnant or breast-feeding women
  15. Sexually active men* or women of childbearing potential** who are unwilling to practice adequate contraception during the study (adequate contraceptive measures include stable use of oral contraceptives or other prescription pharmaceutical contraceptives for 2 or more menstrual cycles prior to screening; intrauterine device [IUD]; bilateral tubal ligation; vasectomy; condom plus contraceptive sponge, foam, or jelly, or diaphragm plus contraceptive sponge, foam, or jelly)
  16. History of hyaluronidase (HA) injection after the diagnosis of thyroid eye disease
  17. Taking part in other research studies in the past 12 months that have involved radiation exposure
  18. Participated in other research studies in the past 12 months that required radiologic imaging (particularly CT scans and not MRIs)

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Hyaluronidase and afliberceptSub-tenon injection of hyaluronidase (HA) followed by a sub-tenon injection of afliberceptGroup 2: Sub-tenon's injection of hyaluronidase (HA) followed by sub-tenon injection of aflibercept
Hyaluronidase aloneSub-tenon injection of hyaluronidase (HA) aloneGroup 3: Sub-tenon injection of HA injection alone
Saline and afliberceptSub-tenon injection of saline followed by a sub-tenon injection of afliberceptGroup 1: Sub-tenon's injection of saline followed by sub-tenon injection of aflibercept
Primary Outcome Measures
NameTimeMethod
Primary Outcome: Safety45 days

To assess the safety and tolerability of sub-tenon aflibercept in combination with either saline or hyaluronidase (HA) in patients with acute Thyroid Eye Disease (TED) as assessed by the incidence and severity of adverse events

Secondary Outcome Measures
NameTimeMethod
Secondary Outcome: Change in Ocular Alignment1-90 days

Change in degree of ocular misalignment during physical exam

Secondary Outcome: Change in Vision measured by Ishihara color test1-90 days

Change in vision as measured by Ishihara color test

Secondary Outcome: Change in Proptosis by CT scan1-90 days

Change in proptosis as measured by CT scan

Secondary Outcome: Change in Ocular Motility1-90 days

Change in limitation in ocular motility as measured with physical examination

Secondary Outcome: Change in Eyelid Retraction/Position1-90 days

Change in eyelid retraction/position as measured by the mm of inferior and superior scleral show on physical examination

Secondary Outcome: SafetyBaseline to day 90

To assess the safety and tolerability of sub-tenon aflibercept in combination with either saline or hyaluronidase (HA) in patients with acute Thyroid Eye Disease (TED) as assessed by the incidence and severity of adverse events

Secondary Outcome: Change in Proptosis measured by exophthalmometry1-90 days

Change in proptosis as measured by Hertel exophthalmometry

Secondary Outcome: Change in Vision measured by ETDRS BCVA1-90 days

Change in vision as measured by the Early Treatment Diabetic Retinopathy Study (ETDRS) Best Corrected Visual Acuity (BCVA)

Secondary Outcome: Change in Visual Function1-90 days

Change in visual function as determined by automated Humphrey visual field

Secondary Outcome: Change in Clinical Activity1-90 days

Change in clinical activity as measured by a 2 point decrease on the clinical activity score (CAS)

Secondary Outcome: Change in Ocular Muscle1-90 days

Change in extra ocular muscle diameter as measured by computed tomography (CT) scan

Secondary Outcome: Change in Pain/Discomfort Reported by Subjects1-90 days

Change in subjective score of pain/discomfort based upon patient Graves' Ophthalmopathy Quality of Life (GO-QOL) questionnaire

Trial Locations

Locations (1)

Mass Eye and Ear

🇺🇸

Boston, Massachusetts, United States

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