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ION356

Generic Name
ION356

Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)

Phase 1
Recruiting
Conditions
Pelizaeus-Merzbacher Disease
Interventions
First Posted Date
2023-11-29
Last Posted Date
2025-05-01
Lead Sponsor
Ionis Pharmaceuticals, Inc.
Target Recruit Count
24
Registration Number
NCT06150716
Locations
🇳🇱

Ionis Investigative Site, Amsterdam, Netherlands

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