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Afegostat

Generic Name
Afegostat
Drug Type
Small Molecule
Chemical Formula
C6H13NO3
CAS Number
169105-89-9
Unique Ingredient Identifier
G23AP190YS

A Study in Type 1 Gaucher Patients to Evaluate the Pharmacokinetics, Safety and Pharmacodynamics of AT2101

Phase 1
Terminated
Conditions
Type 1 Gaucher Disease
Interventions
First Posted Date
2009-04-03
Last Posted Date
2010-08-19
Lead Sponsor
Amicus Therapeutics
Target Recruit Count
1
Registration Number
NCT00875160
Locations
🇺🇸

Comprehensive Phase One, Miramar, Florida, United States

🇬🇧

Guy's Drug Research Unit, London, United Kingdom

A Long-Term Extension Study of AT2101 (Afegostat Tartrate) in Type 1 Gaucher Patients

Phase 2
Completed
Conditions
Gaucher Disease
Type 1 Gaucher Disease
Gaucher Disease, Type 1
Interventions
First Posted Date
2008-12-23
Last Posted Date
2018-08-15
Lead Sponsor
Amicus Therapeutics
Target Recruit Count
8
Registration Number
NCT00813865

A Study of Oral AT2101 (Afegostat Tartrate) in Treatment-naive Patients With Gaucher Disease

Phase 2
Completed
Conditions
Gaucher Disease
Type 1 Gaucher Disease
Gaucher Disease, Type 1
Interventions
First Posted Date
2007-03-13
Last Posted Date
2018-08-15
Lead Sponsor
Amicus Therapeutics
Target Recruit Count
19
Registration Number
NCT00446550

A Study of AT2101 (Afegostat Tartrate) in Adult Patients With Type 1 Gaucher Disease Currently Receiving Enzyme Replacement Therapy

Phase 2
Completed
Conditions
Gaucher Disease, Type 1
Type 1 Gaucher Disease
Gaucher Disease
Interventions
First Posted Date
2007-02-09
Last Posted Date
2018-09-25
Lead Sponsor
Amicus Therapeutics
Target Recruit Count
30
Registration Number
NCT00433147
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