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WVE-006

Generic Name
WVE-006

A Phase 1b/2a, Open-label Single Ascending Doses and Multiple Ascending Doses Study in Participants with Pi*ZZ AATD

Phase 1
Recruiting
Conditions
Alpha-1 Antitrypsin Deficiency
Interventions
First Posted Date
2024-05-08
Last Posted Date
2025-02-10
Lead Sponsor
Wave Life Sciences Ltd.
Target Recruit Count
24
Registration Number
NCT06405633
Locations
🇦🇺

St. Vincent's Hospital, Melbourne, Fitzroy, Victoria, Australia

🇨🇦

Dalhousie University - Queen Elizabeth II Health Sciences Centre, Halifax, Nova Scotia, Canada

🇳🇿

Waikato Hospital, Hamilton, New Zealand

and more 3 locations

A Phase 1 Research Study to Evaluate Safety, Tolerability, and Pharmacokinetics of WVE-006 in Healthy Participants With Wild-type AAT Expression (RestorAATion-1)

Phase 1
Completed
Conditions
Alpha-1 Antitrypsin Deficiency
Interventions
First Posted Date
2024-01-02
Last Posted Date
2025-04-29
Lead Sponsor
Wave Life Sciences Ltd.
Target Recruit Count
47
Registration Number
NCT06186492
Locations
🇬🇧

Simbec-Orion Clinical Pharmacology,, Merthyr Tydfil, Wales, United Kingdom

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