MedPath

BMN-307

Generic Name
BMN-307

AAV Gene Therapy Study for Subjects with PKU

Phase 1
Active, not recruiting
Conditions
Phenylketonuria (PKU)
Interventions
First Posted Date
2020-07-21
Last Posted Date
2024-12-12
Lead Sponsor
BioMarin Pharmaceutical
Target Recruit Count
100
Registration Number
NCT04480567
Locations
🇺🇸

University of South Florida, Tampa, Florida, United States

🇺🇸

Morristown Medical Center, Morristown, New Jersey, United States

🇬🇧

University Hospital Birmingham NHS Foundation Trust, Birmingham, United Kingdom

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