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Baliforsen

Generic Name
Baliforsen
Drug Type
Biotech
CAS Number
1698048-23-5
Unique Ingredient Identifier
DR9CF3915M

A Safety andTolerability Study of Multiple Doses of ISIS-DMPKRx in Adults With Myotonic Dystrophy Type 1

Phase 1
Completed
Conditions
Myotonic Dystrophy Type 1
Interventions
Drug: Placebo
First Posted Date
2014-12-09
Last Posted Date
2022-12-06
Lead Sponsor
Ionis Pharmaceuticals, Inc.
Target Recruit Count
48
Registration Number
NCT02312011
Locations
🇺🇸

Stanford University Medical Center, Stanford, California, United States

🇺🇸

University of Florida, Gainesville, Florida, United States

🇺🇸

Kennedy Krieger Institute, Baltimore, Maryland, United States

and more 5 locations
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