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HST5040

Generic Name
HST5040

Study of HST5040 in Subjects With Propionic or Methylmalonic Acidemia

Phase 2
Terminated
Conditions
Methylmalonic Acidemia
Propionic Acidemia
Interventions
Drug: Placebo
First Posted Date
2021-02-01
Last Posted Date
2024-01-05
Lead Sponsor
HemoShear Therapeutics
Target Recruit Count
26
Registration Number
NCT04732429
Locations
🇺🇸

Rady Children's Hospital, San Diego, California, United States

🇺🇸

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States

🇺🇸

University of Minnesota, Minneapolis, Minnesota, United States

and more 13 locations
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