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Aceneuramic acid

Generic Name
Aceneuramic acid
Drug Type
Small Molecule
Chemical Formula
C11H19NO9
CAS Number
131-48-6
Unique Ingredient Identifier
GZP2782OP0
Background

Aceneuramic acid has been used in trials studying the treatment of Distal Myopathy, Nonaka Type, Hereditary Inclusion Body Myopathy, and Distal Myopathy With Rimmed Vacuoles.

Efficacy Confirmation Study of NPC-09

Phase 3
Completed
Conditions
Distal Myopathy With Rimmed Vacuoles (DMRV)
Hereditary Inclusion Body Myopathy (hIBM)
GNE Myopathy
Nonaka Disease
Interventions
Drug: NPC-09 placebo
First Posted Date
2020-12-17
Last Posted Date
2022-05-16
Lead Sponsor
Nobelpharma
Target Recruit Count
14
Registration Number
NCT04671472
Locations
🇯🇵

National Center Hospital of Neurology and Psychiatry Hospita, Kodaira, Tokyo, Japan

🇯🇵

Kumamoto University Hospital, Kumamoto, Japan

🇯🇵

Nagoya University Hospital, Nagoya, Aichi, Japan

and more 2 locations

Pharmacokinetic Study on N-acetylneuraminic Acid

Phase 1
Completed
Conditions
Nonaka Myopathy
Hereditary Inclusion Body Myopathy
Interventions
First Posted Date
2010-11-09
Last Posted Date
2011-09-08
Lead Sponsor
Tohoku University
Target Recruit Count
6
Registration Number
NCT01236898
Locations
🇯🇵

Tohoku University Hospital, Sendai, Miyagi, Japan

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