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Clinical Trial News

Rising Demand for Comparator Clinical Trials Reshapes Drug Development Landscape

  • Comparator clinical trials are experiencing increased demand driven by market competition, regulatory pressure, and the growing complexity of therapeutic protocols.
  • Supply chain challenges in comparator studies, including product sourcing and logistics, significantly impact trial timelines and require careful planning and risk management.
  • The shift towards comparator trials over placebo-controlled studies is motivated by ethical considerations and regulatory preferences, particularly in evaluating new drugs against existing treatments.

First Immunotherapy Success in Prostate Cancer Shows Promise for DNA Repair-Deficient Tumors

  • A landmark clinical trial demonstrates that pembrolizumab immunotherapy provides survival benefits for a subset of men with advanced, otherwise untreatable prostate cancer.
  • Of 258 men treated with pembrolizumab, 38% remained alive after one year and 11% continued treatment without disease progression.
  • Men with DNA repair gene mutations in their tumors showed higher response rates, suggesting genetic testing could identify optimal candidates for immunotherapy.
  • Researchers are planning a new trial specifically targeting prostate cancer patients with DNA repair mutations to validate this precision medicine approach.

Landmark TAILORx Trial Shows 70% of Early-Stage Breast Cancer Patients Can Safely Skip Chemotherapy

  • The TAILORx trial, involving over 10,000 women, demonstrates that approximately 70% of patients with hormone-receptor positive, HER2-negative early breast cancer can safely avoid chemotherapy when guided by genetic testing.
  • Women over 50 with Oncotype DX recurrence scores of 0-25 showed no significant survival benefit from adding chemotherapy to hormone therapy alone.
  • The findings could spare an estimated 65,000 women annually in the US from chemotherapy's toxic side effects while maintaining excellent long-term outcomes.
  • This precision medicine approach represents the largest breast cancer trial to date and marks a paradigm shift toward personalized treatment strategies.

GSK Partners with Cloud Pharmaceuticals to Accelerate Drug Discovery Through AI Technology

  • GlaxoSmithKline has entered a strategic collaboration with Cloud Pharmaceuticals to leverage AI-driven technology for designing novel small-molecule agents, marking Cloud's first major pharma partnership.
  • Cloud Pharmaceuticals' proprietary AI platform claims to reduce traditional drug discovery timelines from over five years to just a few months, offering significant efficiency gains in lead molecule identification.
  • The partnership follows GSK's $33 million deal with ExScientia and represents the company's first major AI initiative under Chief Digital Officer Karenann Terrell's leadership.

NeuClone Announces Positive Preclinical Results for Stelara® Biosimilar Candidate

  • NeuClone's biosimilar candidate for Stelara® (ustekinumab) shows comparable 3D structure to the reference product through X-ray crystallography.
  • The structural confirmation supports NeuClone's 'Right from the Start®' approach, ensuring high similarity to the original biologic from early development stages.
  • Clinical trials for the Stelara® biosimilar, developed in partnership with Serum Institute of India, are planned to begin in 2019.
  • Stelara®, a monoclonal antibody targeting IL-12 and IL-23, had global sales of $4.0 billion in 2017 and is used to treat conditions like plaque psoriasis and Crohn's disease.

CRISPR Gene Editing Restores Dystrophin Expression in Canine DMD Model

  • Systemic delivery of CRISPR gene editing components restored dystrophin expression in skeletal muscle of DMD dogs, ranging from 3 to 90% of normal levels.
  • Cardiac muscle dystrophin levels reached 92% of normal in the dog receiving the highest dose, demonstrating significant cardiac muscle restoration.
  • Treated dogs exhibited improved muscle histology, indicating a potential therapeutic benefit of gene editing for Duchenne muscular dystrophy.
  • This large-animal study supports the clinical potential of gene editing approaches for treating DMD, warranting further development and clinical translation.

sTMS Shows Promise for Migraine Prevention in Open-Label Study

  • A multicenter, prospective, open-label study suggests that single-pulse transcranial magnetic stimulation (sTMS) may be an effective preventive treatment for migraine.
  • The study demonstrated a statistically significant reduction of 2.75 headache days per month compared to a performance goal (p < 0.0001).
  • 46% of participants experienced a 50% or greater reduction in headache days, alongside reduced acute medication use and improved HIT-6 scores.
  • sTMS was found to be safe and well-tolerated, with no serious adverse events reported during the study period.

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Novartis' Sandoz Partners with Pear Therapeutics to Combat Substance Use Disorders with Digital Solutions

  • Sandoz, a Novartis division, has partnered with Pear Therapeutics to commercialize reSET, the first FDA-approved mobile medical application for treating substance use disorders.
  • The collaboration includes development of reSET-O, a specialized digital therapeutic for opioid use disorder patients undergoing buprenorphine treatment.
  • This strategic partnership expands upon an existing collaboration between Novartis and Pear to develop digital therapeutics for schizophrenia and multiple sclerosis patients.

Alder BioPharmaceuticals to Present New Phase 3 Migraine Prevention Data for Eptinezumab

Alder BioPharmaceuticals announced it will present new Phase 3 data for eptinezumab, its lead investigational product for migraine prevention, at the 70th Annual American Academy of Neurology Meeting. The presentations will include data from the PROMISE 1 and PROMISE 2 clinical trials, highlighting eptinezumab's potential as a treatment option for migraine sufferers.

Blockchain Technology Poised to Transform Pharmaceutical Supply Chain Security and Traceability

  • The pharmaceutical industry is turning to blockchain technology to address critical supply chain challenges including counterfeit drugs, product tracking, and temperature control issues.
  • Blockchain implementation would enable real-time verification of drug authenticity and complete supply chain visibility through secure, transparent recording of transactions between verified stakeholders.
  • Industry leaders are exploring cloud-based networks integrated with blockchain to enhance end-to-end visibility, improve product availability, and optimize inventory management across global pharmaceutical operations.
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