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JCR Pharmaceuticals Co., Ltd.

JCR Pharmaceuticals Co., Ltd. logo
🇯🇵Japan
Ownership
Public
Established
1975-01-01
Employees
934
Market Cap
-
Website
http://www.jcrpharm.co.jp

An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB

Phase 1
Recruiting
Conditions
Mucopolysaccharidosis III-B
Interventions
First Posted Date
2024-07-05
Last Posted Date
2025-02-05
Lead Sponsor
JCR Pharmaceuticals Co., Ltd.
Target Recruit Count
10
Registration Number
NCT06488924
Locations
🇯🇵

Hiroshima University Hospital, Hiroshima, Japan

🇯🇵

University of the Ryukyus Hospital, Okinawa, Japan

🇯🇵

National Center for Child Health and Development, Tokyo, Japan

Phase I/II Study of JR-441 in Patients With Mucopolysaccharidosis Type IIIA

Phase 1
Recruiting
Conditions
Mucopolysaccharidosis III-A
Interventions
First Posted Date
2023-10-23
Last Posted Date
2025-05-14
Lead Sponsor
JCR Pharmaceuticals Co., Ltd.
Target Recruit Count
12
Registration Number
NCT06095388
Locations
🇩🇪

Universitätsklinikum Hamburg-Eppendorf, Hamburg, Germany

An Extension Study of JR-141 to Evaluate the Long-term Safety and Efficacy in Mucopolysaccharidosis Type II (Hunter Syndrome) Subjects

Phase 3
Conditions
Mucopolysaccharidosis II
Interventions
First Posted Date
2022-10-26
Last Posted Date
2025-05-16
Lead Sponsor
JCR Pharmaceuticals Co., Ltd.
Target Recruit Count
80
Registration Number
NCT05594992
Locations
🇺🇸

Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States

🇦🇷

Hospital Universitario Austral, Buenos Aires, Argentina

🇮🇹

Osp. Pediatrico Bambino Gesù, IRCCS, Rome, Italy

and more 6 locations

A Phase III Study of JR-141 in Patients With Mucopolysaccharidosis II (STARLIGHT)

Phase 3
Recruiting
Conditions
Mucopolysaccharidosis II
Interventions
First Posted Date
2020-10-05
Last Posted Date
2025-05-16
Lead Sponsor
JCR Pharmaceuticals Co., Ltd.
Target Recruit Count
80
Registration Number
NCT04573023
Locations
🇺🇸

Phoenix Children's Hospital, Phoenix, Arizona, United States

🇺🇸

UCSF Benioff Children's Hospital Oakland, Oakland, California, United States

🇺🇸

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States

and more 26 locations

An Extension Study of JR-171-101 Study in Patients With Mucopolysaccharidosis Type I (MPS I)

Phase 1
Active, not recruiting
Conditions
Mucopolysaccharidosis I
Interventions
First Posted Date
2020-07-01
Last Posted Date
2025-05-16
Lead Sponsor
JCR Pharmaceuticals Co., Ltd.
Target Recruit Count
14
Registration Number
NCT04453085
Locations
🇯🇵

National Hospital Organization Kokura Medical Center, Kitakyushu, Japan

🇯🇵

Osaka Metropolitan University Hospital, Osaka, Japan

🇺🇸

UCSF Benioff Children's Hospital Oakland, Oakland, California, United States

and more 3 locations

An Extension Study of JR-141 in Patients With Mucopolysaccharidosis Type II

Phase 2
Active, not recruiting
Conditions
Mucopolysaccharidosis II
Interventions
First Posted Date
2020-04-16
Last Posted Date
2024-03-15
Lead Sponsor
JCR Pharmaceuticals Co., Ltd.
Target Recruit Count
27
Registration Number
NCT04348136
Locations
🇯🇵

Fukui Clinical site, Fukui, Japan

🇯🇵

Fukuoka Clinical site 2, Fukuoka, Japan

🇯🇵

Fukuoka Clinical site, Fukuoka, Japan

and more 17 locations

A Study of JR-171 in Patients With Mucopolysaccharidosis I

Phase 1
Completed
Conditions
Mucopolysaccharidosis I
Interventions
Drug: JR-171 (lepunafusp alfa)
First Posted Date
2020-01-13
Last Posted Date
2025-03-19
Lead Sponsor
JCR Pharmaceuticals Co., Ltd.
Target Recruit Count
18
Registration Number
NCT04227600
Locations
🇧🇷

Hospital de Clínicas de Porto Alegre, Porto Alegre, Brazil

🇺🇸

UCSF Benioff Children's Hospital Oakland, Oakland, California, United States

🇯🇵

Fukuoka Children's Hospital, Fukuoka, Japan

and more 3 locations

An Extension Study of JR-141-BR21 in Patients With Mucopolysaccharidosis II

Phase 2
Active, not recruiting
Conditions
Mucopolysaccharidosis II
Interventions
First Posted Date
2018-10-17
Last Posted Date
2023-06-23
Lead Sponsor
JCR Pharmaceuticals Co., Ltd.
Target Recruit Count
19
Registration Number
NCT03708965
Locations
🇧🇷

Grupo de Pesquisa Clínica em Genética Médica - HCPA, Porto Alegre, Brazil

🇧🇷

Igeim - Unifesp, São Paulo, Brazil

A Study of JR-141 in Patients With Mucopolysaccharidosis II

Phase 2
Completed
Conditions
Mucopolysaccharidosis II
Interventions
First Posted Date
2018-06-26
Last Posted Date
2022-11-14
Lead Sponsor
JCR Pharmaceuticals Co., Ltd.
Target Recruit Count
28
Registration Number
NCT03568175
Locations
🇯🇵

Osaka Clinical site, Osaka, Japan

🇯🇵

Saitama Clinical site, Saitama, Japan

🇯🇵

Fukui Clinical site, Fukui, Japan

and more 16 locations

A Study of JR-141 in Patients With Mucopolysaccharidosis II

Phase 2
Completed
Conditions
Mucopolysaccharidosis II
Interventions
First Posted Date
2017-12-02
Last Posted Date
2022-11-14
Lead Sponsor
JCR Pharmaceuticals Co., Ltd.
Target Recruit Count
18
Registration Number
NCT03359213
Locations
🇧🇷

Igeim - Unifesp, São Paulo, Brazil

🇧🇷

Grupo de Pesquisa Clínica em Genética Médica - HCPA, Porto Alegre, Brazil

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