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Grace Science LLC

Grace Science LLC logo
🇺🇸United States
Ownership
Private
Established
2017-01-01
Employees
1
Market Cap
-
Website
http://www.gracesciencellc.com

Safety and Efficacy of GS-100 Gene Therapy in Patients With NGLY1 Deficiency

Phase 1
Recruiting
Conditions
NGLY1 Deficiency
Interventions
Genetic: GS-100
First Posted Date
2024-01-10
Last Posted Date
2025-04-24
Lead Sponsor
Grace Science, LLC
Target Recruit Count
6
Registration Number
NCT06199531
Locations
🇺🇸

Oakland Children's Hospital (UCSF Benioff), Oakland, California, United States

🇺🇸

Columbia University Irving Medical Center, New York, New York, United States

🇺🇸

Texas Children's Hospital (Baylor College of Medicine), Houston, Texas, United States

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