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Transposon Therapeutics, Inc.

Transposon Therapeutics, Inc. logo
🇺🇸United States
Ownership
Holding
Established
2019-01-01
Employees
11
Market Cap
-
Website
http://www.transposonrx.com

Clinical Trials

7

Active:5
Completed:0

Trial Phases

2 Phases

Phase 1:2
Phase 2:5

Drug Approvals

0

Drug Approvals

No drug approvals found

This company may not have drug approvals in our database

Clinical Trials

Distribution across different clinical trial phases (7 trials with phase data)• Click on a phase to view related trials

Phase 2
5 (71.4%)
Phase 1
2 (28.6%)

TPN-101 in Aicardi-Goutières Syndrome (AGS)

Phase 2
Active, not recruiting
Conditions
Aicardi-Goutières Syndrome (AGS)
Interventions
First Posted Date
2022-11-14
Last Posted Date
2025-04-04
Lead Sponsor
Transposon Therapeutics, Inc.
Target Recruit Count
16
Registration Number
NCT05613868
Locations
🇫🇷

Laboratory of Neurogenetics and Neuroinflammation Imagine Institute - INSERM U1163, Paris, France

🇮🇹

Presidio Ospedale dei Bambini [Children's Hospital], Brescia, Italy

🇮🇹

SST Fatebenefratelli Sacco, Milano, Italy

and more 2 locations

A Phase 2a Study of TPN-101 in Patients With C9ORF72 ALS/FTD

Phase 2
Active, not recruiting
Conditions
Amyotrophic Lateral Sclerosis
Frontotemporal Dementia
Interventions
Drug: TPN-101, 400 mg/day
Drug: Placebo
First Posted Date
2021-08-06
Last Posted Date
2023-03-06
Lead Sponsor
Transposon Therapeutics, Inc.
Target Recruit Count
42
Registration Number
NCT04993755
Locations
🇺🇸

University of California San Diego, La Jolla, California, United States

🇺🇸

University of California Irvine - ALS & Neuromuscular Center, Orange, California, United States

🇺🇸

UCSF Neurosciences Clinical Research Unit (NCRU), San Francisco, California, United States

and more 16 locations

A Phase 2a Study of TPN-101 in Patients With Progressive Supranuclear Palsy (PSP)

Phase 2
Active, not recruiting
Conditions
Progressive Supranuclear Palsy
Interventions
Drug: TPN-101, 200 mg/day
Drug: TPN-101, 100 mg/day
Drug: TPN-101, 400 mg/day
Drug: Placebo
First Posted Date
2021-08-06
Last Posted Date
2023-07-13
Lead Sponsor
Transposon Therapeutics, Inc.
Target Recruit Count
40
Registration Number
NCT04993768
Locations
🇺🇸

St. Joseph's Hospital and Medical Center, Barrow Neurological Institute, Phoenix, Arizona, United States

🇺🇸

UC San Diego Altman Clinical And Translational Research Institute, La Jolla, California, United States

🇺🇸

UCSF Neurosciences Clinical Research Unit (NCRU), San Francisco, California, United States

and more 11 locations

News

No news found

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