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RETT SYNDROME RESEARCH TRUST

🇺🇸United States
Ownership
-
Established
2008-01-01
Employees
-
Market Cap
-
Website
https://reverserett.org/

Clinical Trials

5

Active:0
Completed:3

Trial Phases

1 Phases

Phase 2:1

Drug Approvals

0

Drug Approvals

No drug approvals found

This company may not have drug approvals in our database

Clinical Trials

Distribution across different clinical trial phases (1 trials with phase data)• Click on a phase to view related trials

Phase 2
1 (100.0%)

Validating Innovative Biosensors for Rett Autonomic Symptom Tracking

Recruiting
Conditions
Rett Syndrome
First Posted Date
2024-03-29
Last Posted Date
2025-07-03
Lead Sponsor
Rett Syndrome Research Trust
Target Recruit Count
30
Registration Number
NCT06338267
Locations
🇺🇸

Rush University Medical Center, Chicago, Illinois, United States

🇺🇸

Boston Children's Hospital, Boston, Massachusetts, United States

🇺🇸

Baylor College of Medicine, Houston, Texas, United States

Development of the ORCA Communication Measure for Rett Syndrome

Completed
Conditions
Rett Syndrome
First Posted Date
2021-06-09
Last Posted Date
2022-04-22
Lead Sponsor
Rett Syndrome Research Trust
Target Recruit Count
272
Registration Number
NCT04920110
Locations
🇺🇸

Duke University, Durham, North Carolina, United States

The Rett Syndrome Global Registry

Recruiting
Conditions
Rett Syndrome
First Posted Date
2021-05-25
Last Posted Date
2024-11-14
Lead Sponsor
Rett Syndrome Research Trust
Target Recruit Count
5000
Registration Number
NCT04900493
Locations
🇺🇸

Rett Syndrome Research Trust, Trumbull, Connecticut, United States

ASSESSING EMERALD AND MC10 BIOSTAMP nPOINT BIOSENSORS FOR RETT SYNDROME

Completed
Conditions
Rett Syndrome
First Posted Date
2020-08-17
Last Posted Date
2024-11-14
Lead Sponsor
Rett Syndrome Research Trust
Target Recruit Count
21
Registration Number
NCT04514549
Locations
🇺🇸

Boston Children's Hospital, Boston, Massachusetts, United States

A Study to Evaluate Ketamine for the Treatment of Rett Syndrome

Phase 2
Completed
Conditions
Rett Syndrome
Interventions
First Posted Date
2018-08-16
Last Posted Date
2024-05-28
Lead Sponsor
Rett Syndrome Research Trust
Target Recruit Count
23
Registration Number
NCT03633058
Locations
🇺🇸

University of Alabama Birmingham School of Medicine, Birmingham, Alabama, United States

🇺🇸

Children's Hospital Colorado, Aurora, Colorado, United States

🇺🇸

Rush University Medical Center, Chicago, Illinois, United States

and more 4 locations

News

Apertura Gene Therapy Partners with Rett Syndrome Research Trust to Advance Blood-Brain Barrier-Crossing Gene Therapy Platform

Apertura Gene Therapy and Rett Syndrome Research Trust announced a collaboration to license Apertura's TfR1-targeted AAV capsid technology for developing genetic medicines to treat Rett syndrome.

ProQR Advances RNA Editing Pipeline with Four Clinical Readouts Expected by 2026

ProQR Therapeutics is advancing its Axiomer™ RNA editing platform across liver and CNS programs, with its lead program AX-0810 for cholestatic diseases on track for CTA filing in Q2 2025.

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