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FRIEDREICH'S ATAXIA RESEARCH ALLIANCE

๐Ÿ‡บ๐Ÿ‡ธUnited States
Ownership
-
Established
1998-01-01
Employees
-
Market Cap
-
Website
http://www.curefa.org/index.php

Understanding the Natural History Early in the Course or Presentation of Friedreich Ataxia

Not yet recruiting
Conditions
Friedreich Ataxia
Rare Diseases
Interventions
Other: Geneticlly confirmed disease causing FXN mutatuion
Other: Healthy Control
First Posted Date
2024-08-19
Last Posted Date
2024-12-19
Lead Sponsor
Friedreich's Ataxia Research Alliance
Target Recruit Count
300
Registration Number
NCT06560346
Locations
๐Ÿ‡บ๐Ÿ‡ธ

St. Jude Children's Research Hospital, Memphis, Tennessee, United States

๐Ÿ‡บ๐Ÿ‡ธ

University of Iowa, Stead Family Children's Hospital, Iowa City, Iowa, United States

๐Ÿ‡บ๐Ÿ‡ธ

Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States

and more 4 locations

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

Recruiting
Conditions
Friedreich Ataxia
First Posted Date
2023-08-30
Last Posted Date
2025-02-18
Lead Sponsor
Friedreich's Ataxia Research Alliance
Target Recruit Count
3000
Registration Number
NCT06016946
Locations
๐Ÿ‡บ๐Ÿ‡ธ

UCLA Ataxia Center, Los Angeles, California, United States

๐Ÿ‡บ๐Ÿ‡ธ

University of Colorado, Denver, Colorado, United States

๐Ÿ‡บ๐Ÿ‡ธ

University of Florida - Neurology, Gainesville, Florida, United States

and more 31 locations

FA Clinical Outcome Measures

Active, not recruiting
Conditions
Friedreich Ataxia
Neuro-Degenerative Disease
First Posted Date
2017-03-27
Last Posted Date
2024-10-04
Lead Sponsor
Friedreich's Ataxia Research Alliance
Target Recruit Count
2000
Registration Number
NCT03090789
Locations
๐Ÿ‡บ๐Ÿ‡ธ

UCLA Ataxia Center, Los Angeles, California, United States

๐Ÿ‡บ๐Ÿ‡ธ

University of Colorado, Denver, Colorado, United States

๐Ÿ‡บ๐Ÿ‡ธ

University of Florida - Neurology, Gainesville, Florida, United States

and more 11 locations
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