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RECORDATI RARE DISEASES

RECORDATI RARE DISEASES logo
🇫🇷France
Ownership
Private
Established
1990-01-01
Employees
251
Market Cap
-
Website
https://www.recordatirarediseases.com

Cold Agglutinin Disease Real World Evidence Registry

Recruiting
Conditions
Cold Agglutinin Disease (CAD)
Cold Agglutinin Syndrome (CAS)
Interventions
First Posted Date
2023-03-30
Last Posted Date
2025-05-01
Lead Sponsor
Recordati Rare Diseases
Target Recruit Count
400
Registration Number
NCT05791708
Locations
🇮🇹

Investigational Site Number : 3405, Terni, Italy

🇫🇷

Investigational Site Number : 3203, Pessac, France

🇮🇹

Investigational Site Number : 3412, Ravenna, Italy

and more 65 locations

An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics

Recruiting
Conditions
Hyperammonemia
Methylmalonic Acidemia
Propionic Acidemia
Interventions
First Posted Date
2021-09-10
Last Posted Date
2025-04-15
Lead Sponsor
Recordati Rare Diseases
Target Recruit Count
20
Registration Number
NCT05040178
Locations
🇺🇸

Children's National Hospital, Washington, District of Columbia, United States

🇺🇸

University of South Florida, Tampa, Florida, United States

🇺🇸

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States

and more 2 locations

REC 0/0559 Eye Drops for Treatment of Moderate and Severe Neurotrophic Keratitis in Adult Patients

Phase 2
Completed
Conditions
Neurotrophic Keratitis
Interventions
Other: Vehicle
First Posted Date
2020-02-19
Last Posted Date
2025-05-14
Lead Sponsor
Recordati Rare Diseases
Target Recruit Count
108
Registration Number
NCT04276558
Locations
🇺🇸

University of Florida, Gainesville, Florida, United States

🇺🇸

University of Maryland School of Medicine UMSOM, Baltimore, Maryland, United States

🇮🇹

Università Magna Grecia di Catanzaro, Germaneto, Calabria, Italy

and more 38 locations

Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods Approach

Recruiting
Conditions
Methylmalonic Acidemia
Propionic Acidemia
Interventions
First Posted Date
2019-11-25
Last Posted Date
2024-02-05
Lead Sponsor
Recordati Rare Diseases
Target Recruit Count
95
Registration Number
NCT04176523
Locations
🇫🇷

Hopital de Hautepierre, Strasbourg, France

🇮🇹

Azienda Ospedaliero Universitaria Meyer, Firenze, Italy

🇩🇪

Klinikum Bremen Mitte, Prof. Hess Kinderklinik, Bremen, Germany

and more 29 locations

Cystadrops in Pediatric Cystinosis Patients From Six Months to Less Than Two Years Old (SCOB2)

Phase 3
Completed
Conditions
Cystinosis
Interventions
First Posted Date
2019-10-14
Last Posted Date
2024-02-05
Lead Sponsor
Recordati Rare Diseases
Target Recruit Count
5
Registration Number
NCT04125927
Locations
🇧🇪

UZ Leuven, Leuven, Belgium

🇫🇷

Hôpital Necker-Enfants Malades, Paris, France

🇬🇧

Great Ormond Street Hospital, London, United Kingdom

and more 3 locations
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