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Bioblast Pharma Ltd.

Bioblast Pharma Ltd. logo
🇮🇱Israel
Ownership
Public, Subsidiary
Established
2012-01-01
Employees
11
Market Cap
-
Website
http://bioblast-pharma.com

Clinical Trials

5

Active:0
Completed:4

Trial Phases

3 Phases

Phase 1:1
Phase 2:3
Phase 3:1

Drug Approvals

0

Drug Approvals

No drug approvals found

This company may not have drug approvals in our database

Clinical Trials

Distribution across different clinical trial phases (5 trials with phase data)• Click on a phase to view related trials

Phase 2
3 (60.0%)
Phase 1
1 (20.0%)
Phase 3
1 (20.0%)

Treatment of Oculopharyngeal Muscular Dystrophy With Trehalose

Phase 2
Withdrawn
Conditions
Oculopharyngeal Muscular Dystrophy
Interventions
First Posted Date
2020-01-13
Last Posted Date
2020-01-13
Lead Sponsor
Bioblast Pharma Ltd.
Registration Number
NCT04226924
Locations
🇨🇦

Ecogene-21, Chicoutimi, Quebec, Canada

🇨🇦

Montreal Neurological Institute and Hospital, Montréal, Quebec, Canada

🇨🇦

CHU de Québec-Université Laval- Hôpital Enfant-Jésus, Québec, Quebec, Canada

A Study to Establish Safety and Maximum Tolerated Dose of IV Trehalose in Healthy Subjects

Phase 1
Completed
Conditions
Healthy Volunteer Subjects
Interventions
First Posted Date
2016-04-01
Last Posted Date
2016-11-22
Lead Sponsor
Bioblast Pharma Ltd.
Target Recruit Count
24
Registration Number
NCT02725957
Locations
🇺🇸

PAREXEL Baltimore Early Phase Clinical Unit; Harbor Hospital, Baltimore, Maryland, United States

Continuation Protocol to Protocol BBCO-001

Phase 3
Completed
Conditions
Muscular Dystrophy, Oculopharyngeal (OPMD)
Interventions
Drug: Tehalose 30gr
First Posted Date
2014-12-31
Last Posted Date
2019-07-17
Lead Sponsor
Bioblast Pharma Ltd.
Target Recruit Count
9
Registration Number
NCT02328482
Locations
🇨🇦

Montreal Neurological Institute, McGill University, Montreal, Quebec, Canada

Study To Assess Safety, Tolerability and Efficacy of Intravenous Cabaletta in Patients With Machado-Joseph Disease

Phase 2
Completed
Conditions
Machado-Joseph Disease / Spinocerebellar Ataxia 3
Interventions
First Posted Date
2014-05-28
Last Posted Date
2016-11-22
Lead Sponsor
Bioblast Pharma Ltd.
Target Recruit Count
15
Registration Number
NCT02147886
Locations
🇮🇱

Meir Medical Center, Kfar Saba, Israel

Safety Tolerability and Efficacy Study of Cabaletta to Treat Oculopharyngeal Muscular Dystrophy (OPMD) Patients

Phase 2
Completed
Conditions
Oculopharyngeal Muscular Dystrophy
Interventions
First Posted Date
2013-12-19
Last Posted Date
2017-10-17
Lead Sponsor
Bioblast Pharma Ltd.
Target Recruit Count
25
Registration Number
NCT02015481
Locations
🇺🇸

UCLA, Los Angeles, California, United States

🇺🇸

Tahseen Mozaffar, Orange, California, United States

🇨🇦

Montreal Neurological Institute, McGill University, Montreal, Quebec, Canada

and more 1 locations

News

No news found

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