MedPath

Rare Disease Research, LLC

Ownership
Private
Employees
-
Market Cap
-
Website

Clinical Trials

1

Active:0
Completed:0

Trial Phases

1 Phases

Phase 4:1

Drug Approvals

0

Drug Approvals

No drug approvals found

This company may not have drug approvals in our database

Clinical Trials

Distribution across different clinical trial phases (1 trials with phase data)• Click on a phase to view related trials

Phase 4
1 (100.0%)

An Open-Label Study of Golodirsen in Non-Ambulant Patients With Duchenne Muscular Dystrophy

Phase 4
Terminated
Conditions
Duchenne Muscular Dystrophy
Interventions
First Posted Date
2021-01-13
Last Posted Date
2021-05-17
Lead Sponsor
Rare Disease Research, LLC
Target Recruit Count
2
Registration Number
NCT04708314
Locations
🇺🇸

Rare Disease Research, LLC, Atlanta, Georgia, United States

🇺🇸

Children's Hospital of Pittsburgh of UPMC, Pittsburgh, Pennsylvania, United States

News

No news found

MedPath

Empowering clinical research with data-driven insights and AI-powered tools.

© 2025 MedPath, Inc. All rights reserved.