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Neuren Pharmaceuticals, Inc.

๐Ÿ‡บ๐Ÿ‡ธUnited States
Ownership
-
Employees
-
Market Cap
$1.3B
Website

Clinical Trials

13

Active:0
Completed:11

Trial Phases

2 Phases

Phase 1:3
Phase 2:10

Drug Approvals

0

Drug Approvals

No drug approvals found

This company may not have drug approvals in our database

Clinical Trials

Distribution across different clinical trial phases (13 trials with phase data)โ€ข Click on a phase to view related trials

Phase 2
10 (76.9%)
Phase 1
3 (23.1%)

An Open-Label Study of Oral NNZ-2591 in Prader-Willi Syndrome (PWS-001)

Phase 2
Withdrawn
Conditions
Prader-Willi Syndrome
Interventions
First Posted Date
2023-05-30
Last Posted Date
2024-12-09
Lead Sponsor
Neuren Pharmaceuticals Limited
Target Recruit Count
20
Registration Number
NCT05879614
Locations
๐Ÿ‡บ๐Ÿ‡ธ

Rady Children's Hospital San Diego, San Diego, California, United States

๐Ÿ‡บ๐Ÿ‡ธ

Rare Disease Research, Atlanta, Georgia, United States

๐Ÿ‡บ๐Ÿ‡ธ

Uncommon Cures, Chevy Chase, Maryland, United States

and more 1 locations

An Open-Label Study of Oral NNZ-2591 in Phelan-McDermid Syndrome (PMS-001)

Phase 2
Completed
Conditions
Phelan-McDermid Syndrome
Interventions
First Posted Date
2021-08-27
Last Posted Date
2025-06-03
Lead Sponsor
Neuren Pharmaceuticals Limited
Target Recruit Count
18
Registration Number
NCT05025241
Locations
๐Ÿ‡บ๐Ÿ‡ธ

Rush University Medical Center, Chicago, Illinois, United States

๐Ÿ‡บ๐Ÿ‡ธ

Massachusetts General Hospital, Boston, Massachusetts, United States

๐Ÿ‡บ๐Ÿ‡ธ

Boston Children's Hospital, Boston, Massachusetts, United States

and more 1 locations

An Open-Label Study of Oral NNZ-2591 in Pitt Hopkins Syndrome (PTHS-001)

Phase 2
Completed
Conditions
Pitt Hopkins Syndrome
Interventions
First Posted Date
2021-08-27
Last Posted Date
2025-06-18
Lead Sponsor
Neuren Pharmaceuticals Limited
Target Recruit Count
28
Registration Number
NCT05025332
Locations
๐Ÿ‡บ๐Ÿ‡ธ

University of Alabama at Birmingham, Birmingham, Alabama, United States

๐Ÿ‡บ๐Ÿ‡ธ

University of California at San Francisco, San Francisco, California, United States

๐Ÿ‡บ๐Ÿ‡ธ

Children's Hospital Colorado, Aurora, Colorado, United States

and more 2 locations

An Open-Label Study of the Safety, Tolerability, and Pharmacokinetics of Oral NNZ-2591 in Angelman Syndrome

Phase 2
Completed
Conditions
Angelman Syndrome
Interventions
First Posted Date
2021-08-18
Last Posted Date
2025-01-31
Lead Sponsor
Neuren Pharmaceuticals Limited
Target Recruit Count
17
Registration Number
NCT05011851
Locations
๐Ÿ‡ฆ๐Ÿ‡บ

Sydney Children's Hospital, Randwick, New South Wales, Australia

๐Ÿ‡ฆ๐Ÿ‡บ

Centre for Clinical Trials in Rare Neurodevelopmental Disorders at Children's Health Queensland Hospital and Health Service, South Brisbane, Queensland, Australia

๐Ÿ‡ฆ๐Ÿ‡บ

Austin Health, Heidelberg, Victoria, Australia

To Evaluate the Safety, Tolerability and Pharmacokinetics of Oral NNZ-2591 in Healthy Volunteers

Phase 1
Completed
Conditions
Healthy Volunteers
Interventions
Drug: Placebo
First Posted Date
2020-05-08
Last Posted Date
2021-07-09
Lead Sponsor
Neuren Pharmaceuticals Limited
Target Recruit Count
28
Registration Number
NCT04379869
Locations
๐Ÿ‡ฆ๐Ÿ‡บ

Scientia Clinical Research, Sydney, New South Wales, Australia

๐Ÿ‡ฆ๐Ÿ‡บ

Linear Clinical Research, The Queen Elizabeth II Medical Centre, Nedlands, Western Australia, Australia

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News

Ionis Advances Antisense Therapy for Angelman Syndrome to Phase 3 Following Promising Clinical Results

Ionis Pharmaceuticals is moving forward with Phase 3 trials for ION582, an antisense therapy designed to unsilence the paternal UBE3A gene in Angelman syndrome patients, after Biogen declined to license the drug.

FDA Grants Fast Track Status to Neuren's Novel Pitt Hopkins Syndrome Treatment

Neuren Pharmaceuticals receives FDA Fast Track designation for their investigational treatment targeting Pitt Hopkins syndrome, a rare neurodevelopmental disorder affecting 1 in 34,000-41,000 people.

Immutep's LAG-3 Agonist Shows Promise, Percheron and PYC Update on Neurological Disease Trials

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ASX Biotechs Gear Up for Critical Phase III Trial Results in 2025

Several ASX-listed biotech companies are anticipating crucial Phase III clinical trial results in 2025, which could significantly impact their market value and future prospects.

Imugene's Azer-Cel Trial Opens First Australian Site; Neuren's Daybue Sales Exceed Expectations

Imugene has initiated its Phase 1b clinical trial for azer-cel in Australia, marking a key advancement in its allogeneic CAR T-cell therapy development.

Acadia Pharmaceuticals Secures $150M in Priority Review Voucher Sale, Setting High Benchmark

Acadia Pharmaceuticals has successfully sold its FDA priority review voucher for $150 million, marking one of the highest valuations for such vouchers in recent transactions.

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