Clinical Trials
13
Trial Phases
2 Phases
Drug Approvals
0
Drug Approvals
No drug approvals found
This company may not have drug approvals in our database
Clinical Trials
Distribution across different clinical trial phases (13 trials with phase data)β’ Click on a phase to view related trials
An Open-Label Study of Oral NNZ-2591 in Prader-Willi Syndrome (PWS-001)
- First Posted Date
- 2023-05-30
- Last Posted Date
- 2024-12-09
- Lead Sponsor
- Neuren Pharmaceuticals Limited
- Target Recruit Count
- 20
- Registration Number
- NCT05879614
- Locations
- πΊπΈ
Rady Children's Hospital San Diego, San Diego, California, United States
πΊπΈRare Disease Research, Atlanta, Georgia, United States
πΊπΈUncommon Cures, Chevy Chase, Maryland, United States
An Open-Label Study of Oral NNZ-2591 in Phelan-McDermid Syndrome (PMS-001)
- First Posted Date
- 2021-08-27
- Last Posted Date
- 2025-06-03
- Lead Sponsor
- Neuren Pharmaceuticals Limited
- Target Recruit Count
- 18
- Registration Number
- NCT05025241
- Locations
- πΊπΈ
Rush University Medical Center, Chicago, Illinois, United States
πΊπΈMassachusetts General Hospital, Boston, Massachusetts, United States
πΊπΈBoston Children's Hospital, Boston, Massachusetts, United States
An Open-Label Study of Oral NNZ-2591 in Pitt Hopkins Syndrome (PTHS-001)
- First Posted Date
- 2021-08-27
- Last Posted Date
- 2025-06-18
- Lead Sponsor
- Neuren Pharmaceuticals Limited
- Target Recruit Count
- 28
- Registration Number
- NCT05025332
- Locations
- πΊπΈ
University of Alabama at Birmingham, Birmingham, Alabama, United States
πΊπΈUniversity of California at San Francisco, San Francisco, California, United States
πΊπΈChildren's Hospital Colorado, Aurora, Colorado, United States
An Open-Label Study of the Safety, Tolerability, and Pharmacokinetics of Oral NNZ-2591 in Angelman Syndrome
- First Posted Date
- 2021-08-18
- Last Posted Date
- 2025-01-31
- Lead Sponsor
- Neuren Pharmaceuticals Limited
- Target Recruit Count
- 17
- Registration Number
- NCT05011851
- Locations
- π¦πΊ
Sydney Children's Hospital, Randwick, New South Wales, Australia
π¦πΊCentre for Clinical Trials in Rare Neurodevelopmental Disorders at Children's Health Queensland Hospital and Health Service, South Brisbane, Queensland, Australia
π¦πΊAustin Health, Heidelberg, Victoria, Australia
To Evaluate the Safety, Tolerability and Pharmacokinetics of Oral NNZ-2591 in Healthy Volunteers
- First Posted Date
- 2020-05-08
- Last Posted Date
- 2021-07-09
- Lead Sponsor
- Neuren Pharmaceuticals Limited
- Target Recruit Count
- 28
- Registration Number
- NCT04379869
- Locations
- π¦πΊ
Scientia Clinical Research, Sydney, New South Wales, Australia
π¦πΊLinear Clinical Research, The Queen Elizabeth II Medical Centre, Nedlands, Western Australia, Australia
- Prev
- 1
- 2
- 3
- Next
News
Neuren Pharmaceuticals Launches First-Ever Phase 3 Trial for Phelan-McDermid Syndrome
Neuren Pharmaceuticals has initiated the first investigational site in the United States for its Phase 3 clinical trial of NNZ-2591 for Phelan-McDermid syndrome, marking the first-ever Phase 3 trial for this severe neurodevelopmental disorder.
Ionis Advances Antisense Therapy for Angelman Syndrome to Phase 3 Following Promising Clinical Results
Ionis Pharmaceuticals is moving forward with Phase 3 trials for ION582, an antisense therapy designed to unsilence the paternal UBE3A gene in Angelman syndrome patients, after Biogen declined to license the drug.
FDA Grants Fast Track Status to Neuren's Novel Pitt Hopkins Syndrome Treatment
Neuren Pharmaceuticals receives FDA Fast Track designation for their investigational treatment targeting Pitt Hopkins syndrome, a rare neurodevelopmental disorder affecting 1 in 34,000-41,000 people.
Immutep's LAG-3 Agonist Shows Promise, Percheron and PYC Update on Neurological Disease Trials
Immutep's IMP-761, a LAG-3 agonist, demonstrates a favorable safety profile in Phase I trials, potentially addressing autoimmune diseases like rheumatoid arthritis.
ASX Biotechs Gear Up for Critical Phase III Trial Results in 2025
Several ASX-listed biotech companies are anticipating crucial Phase III clinical trial results in 2025, which could significantly impact their market value and future prospects.
Imugene's Azer-Cel Trial Opens First Australian Site; Neuren's Daybue Sales Exceed Expectations
Imugene has initiated its Phase 1b clinical trial for azer-cel in Australia, marking a key advancement in its allogeneic CAR T-cell therapy development.
Acadia Pharmaceuticals Secures $150M in Priority Review Voucher Sale, Setting High Benchmark
Acadia Pharmaceuticals has successfully sold its FDA priority review voucher for $150 million, marking one of the highest valuations for such vouchers in recent transactions.