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NEUROGENE INC.

NEUROGENE INC. logo
πŸ‡ΊπŸ‡ΈUnited States
Ownership
Private, Subsidiary
Established
2003-12-01
Employees
56
Market Cap
-
Website
https://www.neoleukin.com

Clinical Trials

6

Active:1
Completed:2

Trial Phases

2 Phases

Phase 1:2
Not Applicable:1

Drug Approvals

0

Drug Approvals

No drug approvals found

This company may not have drug approvals in our database

Clinical Trials

Distribution across different clinical trial phases (3 trials with phase data)β€’ Click on a phase to view related trials

Phase 1
2 (66.7%)
Not Applicable
1 (33.3%)

A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome

Not Applicable
Recruiting
Conditions
Rett Syndrome
First Posted Date
2023-06-12
Last Posted Date
2025-11-10
Lead Sponsor
Neurogene Inc.
Target Recruit Count
33
Registration Number
NCT05898620
Locations
πŸ‡ΊπŸ‡Έ

University of Alabama at Birmingham, Birmingham, Alabama, United States

πŸ‡ΊπŸ‡Έ

UCSF Benioff Children's Hospital Oakland, Oakland, California, United States

πŸ‡ΊπŸ‡Έ

Nicklaus Children's Hospital Research Institute, Miami, Florida, United States

and more 12 locations

Gene Therapy Study for Children With CLN5 Batten Disease

Phase 1
Active, not recruiting
Conditions
Neuronal Ceroid Lipofuscinosis CLN5
First Posted Date
2022-02-08
Last Posted Date
2024-08-12
Lead Sponsor
Neurogene Inc.
Target Recruit Count
6
Registration Number
NCT05228145
Locations
πŸ‡ΊπŸ‡Έ

University of Rochester, Rochester, New York, United States

πŸ‡¬πŸ‡§

Great Ormond Street Hospital for Children, London, United Kingdom

NL-201 Monotherapy and in Combination With Pembrolizumab in Patients With Relapsed or Refractory Cancer

Phase 1
Completed
Conditions
Advanced Solid Tumor
Solid Tumor
Interventions
First Posted Date
2020-12-09
Last Posted Date
2024-09-30
Lead Sponsor
Neurogene Inc.
Target Recruit Count
59
Registration Number
NCT04659629
Locations
πŸ‡ΊπŸ‡Έ

Memorial Sloan Kettering Cancer Center, New York, New York, United States

πŸ‡ΊπŸ‡Έ

Providence Cancer Center Oncology and Hematology Care Clinic, Portland, Oregon, United States

πŸ‡ΊπŸ‡Έ

UT- MD Anderson, Houston, Texas, United States

and more 5 locations

A Natural History Study of Aspartylglucosaminuria

Terminated
Conditions
Aspartylglucosaminuria
Aspartylglucosamidase (AGA) Deficiency
Lysosomal Storage Diseases
First Posted Date
2019-02-26
Last Posted Date
2022-04-12
Lead Sponsor
Neurogene Inc.
Target Recruit Count
8
Registration Number
NCT03853876
Locations
πŸ‡ΊπŸ‡Έ

University of Texas Southwestern, Dallas, Texas, United States

A Natural History Study of Neuronal Ceroid Lipofuscinosis Type 5 (CLN5)

Completed
Conditions
Ceroid Lipofuscinosis, Neuronal 5
First Posted Date
2019-01-30
Last Posted Date
2024-06-27
Lead Sponsor
Neurogene Inc.
Target Recruit Count
37
Registration Number
NCT03822650
Locations
πŸ‡ΊπŸ‡Έ

University of Rochester Medical Center, Rochester, New York, United States

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