Clinical Trials
4
Trial Phases
2 Phases
Drug Approvals
0
Drug Approvals
No drug approvals found
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Clinical Trials
Distribution across different clinical trial phases (4 trials with phase data)• Click on a phase to view related trials
Adrabetadex to Treat Niemann-Pick Type C1 (NPC1) Disease
- First Posted Date
- 2021-07-12
- Last Posted Date
- 2023-08-29
- Lead Sponsor
- Mandos LLC
- Target Recruit Count
- 66
- Registration Number
- NCT04958642
- Locations
- 🇺🇸
University of Alabama at Birmingham, Birmingham, Alabama, United States
🇺🇸Children's Hospital of Orange County: CHOC Children's, Orange, California, United States
🇺🇸University of California San Francisco, San Francisco, California, United States
Open-label Study of VTS-270 in Participants With Neurologic Manifestations of Niemann-Pick Type C1
- First Posted Date
- 2019-03-19
- Last Posted Date
- 2023-12-26
- Lead Sponsor
- Mandos LLC
- Target Recruit Count
- 2
- Registration Number
- NCT03879655
- Locations
- 🇨🇷
Hospital Clinica Biblica, San José, Costa Rica
Niemann-Pick Type C Treatment With Adrabetadex for Symptoms of Brain and Nervous System
- First Posted Date
- 2018-08-23
- Last Posted Date
- 2024-01-17
- Lead Sponsor
- Mandos LLC
- Target Recruit Count
- 27
- Registration Number
- NCT03643562
- Locations
- 🇺🇸
University of Arkansas System, Little Rock, Arkansas, United States
🇺🇸Loma Linda University Health System, Loma Linda, California, United States
🇺🇸Children's Hospital Los Angeles, Los Angeles, California, United States
VTS-270 to Treat Niemann-Pick Type C1 (NPC1) Disease
- Conditions
- Niemann-Pick Disease, Type C
- First Posted Date
- 2015-08-28
- Last Posted Date
- 2023-02-22
- Lead Sponsor
- Mandos LLC
- Target Recruit Count
- 56
- Registration Number
- NCT02534844
- Locations
- 🇺🇸
University of Alabama at Birmingham, Birmingham, Alabama, United States
🇺🇸Children's Hospital of Orange County, Orange, California, United States
🇺🇸University of California San Francisco, San Francisco, California, United States