Clinical Trials
0
Active:0
Completed:0
Trial Phases
0 Phases
Drug Approvals
5
SFDA:3
FDA:2
Drug Approvals
Clinical Trials
No trials found
News
FDA Approves First Treatment for Alkaptonuria: Nitisinone Shows Clinical Benefits in Rare Metabolic Disorder
The FDA approved nitisinone (Harliku) as the first and only treatment for alkaptonuria, a rare genetic metabolic disorder affecting 1 in 250,000 to 1 million Americans.
Cycle Pharmaceuticals Launches VENXXIVA for Cystinuria Treatment in the US
Cycle Pharmaceuticals has launched VENXXIVA (tiopronin) Delayed-Release Tablets for treating cystinuria in the US, partnering with Torrent Pharma and Vanscoy Rare Pharmacy for distribution.