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BIOCRYST PHARMACEUTICALS, INC.

BIOCRYST PHARMACEUTICALS, INC. logo
🇺🇸United States
Ownership
Public
Established
1986-01-01
Employees
536
Market Cap
$1.7B
Website
http://www.biocryst.com

Clinical Trials

87

Active:32
Completed:41

Trial Phases

3 Phases

Phase 1:30
Phase 2:22
Phase 3:15

Drug Approvals

1

FDA:1

Drug Approvals

Rapivab

Approval Date
Nov 14, 2022
FDA

Clinical Trials

Distribution across different clinical trial phases (67 trials with phase data)• Click on a phase to view related trials

Phase 1
30 (44.8%)
Phase 2
22 (32.8%)
Phase 3
15 (22.4%)

A Study of the Safety, Tolerability, Pharmacokinetics, and Immunogenicity of BCX17725

Phase 1
Recruiting
Conditions
Netherton Syndrome
Interventions
Drug: Placebo
First Posted Date
2024-08-06
Last Posted Date
2025-08-08
Lead Sponsor
BioCryst Pharmaceuticals
Target Recruit Count
66
Registration Number
NCT06539507
Locations
🇦🇺

Investigative site, Brisbane, Queensland, Australia

Dose Escalation of BCX10013 in Participants with Paroxysmal Nocturnal Hemoglobinuria (PNH)

Phase 1
Completed
Conditions
Paroxysmal Nocturnal Hemoglobinuria
Interventions
First Posted Date
2023-10-25
Last Posted Date
2025-01-08
Lead Sponsor
BioCryst Pharmaceuticals
Target Recruit Count
8
Registration Number
NCT06100900
Locations
🇿🇦

BioCryst Investigative Site, Pretoria, South Africa

Long-term Safety of BCX9930 in Participants With Paroxysmal Nocturnal Hemoglobinuria

Phase 2
Terminated
Conditions
Paroxysmal Nocturnal Hemoglobinuria
Interventions
First Posted Date
2023-02-23
Last Posted Date
2025-07-10
Lead Sponsor
BioCryst Pharmaceuticals
Target Recruit Count
28
Registration Number
NCT05741346
Locations
🇬🇧

Investigative Site, London, United Kingdom

Berotralstat Treatment in Children With Hereditary Angioedema

Phase 3
Active, not recruiting
Conditions
Hereditary Angioedema
Pediatric
Interventions
First Posted Date
2022-07-12
Last Posted Date
2024-10-15
Lead Sponsor
BioCryst Pharmaceuticals
Target Recruit Count
29
Registration Number
NCT05453968
Locations
🇬🇧

Investigative Site #1, Bristol, United Kingdom

🇫🇷

Investigative Site #3, Grenoble, France

🇪🇸

Investigative Site #2, Málaga, Spain

Study to Evaluate the Safety, Tolerability of BCX9930 in Participants With Either Complement 3 Glomerulopathy (C3G), Immunoglobulin A Nephropathy (IgAN), or Primary Membranous Nephropathy (PMN)

Phase 2
Terminated
Conditions
Complement 3 Glomerulopathy
Immunoglobulin A Nephropathy
Membranous Nephropathy
Interventions
First Posted Date
2021-12-17
Last Posted Date
2024-05-02
Lead Sponsor
BioCryst Pharmaceuticals
Target Recruit Count
2
Registration Number
NCT05162066
Locations
🇬🇧

Investigative Site, Oxford, United Kingdom

🇪🇸

Investigative Site #1, Madrid, Spain

🇪🇸

Investigative Site #2, Madrid, Spain

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News

Major Pharmaceutical Companies Face Surge in Generic Drug Patent Challenges in Early 2025

Major pharmaceutical companies including AstraZeneca, Novartis, and Astellas are defending patents for blockbuster drugs like Lynparza, Entresto, and Xtandi against generic manufacturers in early 2025.

BioCryst Names Charlie Gayer as New CEO Following Jon Stonehouse's Retirement Announcement

BioCryst Pharmaceuticals announced that CEO Jon Stonehouse will retire on December 31, 2025, with current Chief Commercial Officer Charlie Gayer set to succeed him as president in August and CEO in January 2026.

BioCryst Pharmaceuticals Appoints Babar Ghias as CFO and Head of Corporate Development

BioCryst Pharmaceuticals has appointed Babar Ghias as chief financial officer and head of corporate development, bringing extensive deal-making experience from rare disease companies.

BioCryst Pharmaceuticals Divests European ORLADEYO Rights for $264 Million to Achieve Debt-Free Status

BioCryst Pharmaceuticals sold its European commercial rights to ORLADEYO, a C1 inhibitor therapy for hereditary angioedema, to Neopharmed Gentili for up to $264 million on June 27, 2025.

IgA Nephropathy Pipeline Shows Robust Growth with 30+ Therapies in Development

DelveInsight's 2025 pipeline analysis reveals over 30 companies developing 30+ therapies for IgA nephropathy treatment, representing a robust therapeutic landscape.

BioCryst's Orladeyo Demonstrates Safety and Efficacy in Pediatric Hereditary Angioedema Trial

Interim analysis of APeX-P trial shows Orladeyo (berotralstat) oral granule formulation is safe and well-tolerated in children aged 2-12 years with hereditary angioedema.

BioCryst's Orladeyo® (berotralstat) Receives Recommendation in Ireland for HAE Prophylaxis

The Health Services Executive (HSE) in Ireland has recommended Orladeyo® (berotralstat) for routine prevention of recurrent hereditary angioedema (HAE) attacks in eligible patients 12 years and older.

Clearside Biomedical's CLS-AX Phase IIb Trial Readout Anticipated in Q3 2024

• Clearside Biomedical anticipates primary data readout from its Phase IIb ODYSSEY trial of CLS-AX for wet AMD in Q3 2024, assessing its potential as a maintenance therapy. • The company's SCS Microinjector continues to demonstrate benefits in suprachoroidal drug delivery, with multiple partnerships and clinical trials underway for various indications. • A new collaboration with BioCryst Pharmaceuticals will utilize Clearside's SCS Microinjector to deliver their compound aboard Elestat for treating diabetic macular edema. • Clearside Biomedical's cash balance, including proceeds from a recent offering, is expected to fund operations into Q3 2025, supporting the CLS-AX Phase III program.

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