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Retrotope, Inc.

Retrotope, Inc. logo
๐Ÿ‡บ๐Ÿ‡ธUnited States
Ownership
Subsidiary
Established
2006-01-01
Employees
1
Market Cap
-
Website
http://www.retrotope.com

RT001 in Patients With Progressive Supranuclear Palsy (PSP) PROGRESSIVE SUPRANUCLEAR PALSY

Phase 2
Conditions
Progressive Supranuclear Palsy
Interventions
Drug: Placebo
First Posted Date
2021-06-24
Last Posted Date
2021-06-25
Lead Sponsor
Retrotope, Inc.
Target Recruit Count
40
Registration Number
NCT04937530
Locations
๐Ÿ‡ฉ๐Ÿ‡ช

Agaharied Teaching Hospital, University of Munich, Munich, MD, Germany

RT001 in Amyotrophic Lateral Sclerosis

Phase 2
Conditions
Amyotrophic Lateral Sclerosis
Interventions
Drug: Placebo
First Posted Date
2021-02-21
Last Posted Date
2022-04-08
Lead Sponsor
Retrotope, Inc.
Target Recruit Count
40
Registration Number
NCT04762589
Locations
๐Ÿ‡ณ๐Ÿ‡ฑ

UMC Utrecht, Utrecht, Netherlands

๐Ÿ‡ฑ๐Ÿ‡ป

Riga Stradins Universtiy, Riga, Latvia

๐Ÿ‡ธ๐Ÿ‡ช

Karolinska, Stockholm, Sweden

and more 1 locations

A Study to Assess Efficacy, Long Term Safety and Tolerability of RT001 in Subjects With Friedreich's Ataxia

Phase 3
Completed
Conditions
Friedreich's Ataxia
Interventions
Drug: Placebo
First Posted Date
2019-09-25
Last Posted Date
2022-05-27
Lead Sponsor
Retrotope, Inc.
Target Recruit Count
65
Registration Number
NCT04102501
Locations
๐Ÿ‡บ๐Ÿ‡ธ

Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States

๐Ÿ‡บ๐Ÿ‡ธ

Collaborative Neuroscience Network, LLC, Long Beach, California, United States

๐Ÿ‡บ๐Ÿ‡ธ

University of Iowa Stead Family Children's Hospital, Iowa City, Iowa, United States

and more 3 locations

A Natural History Study of Infantile Neuroaxonal Dystrophy

Completed
Conditions
Neuroaxonal Dystrophy, Infantile
First Posted Date
2019-07-22
Last Posted Date
2022-04-08
Lead Sponsor
Retrotope, Inc.
Target Recruit Count
43
Registration Number
NCT04027816
Locations
๐Ÿ‡จ๐Ÿ‡ณ

Peking University First Hospital, Beijing, China

๐Ÿ‡ช๐Ÿ‡ฌ

National Research Centre, Cairo, Egypt

๐Ÿ‡ธ๐Ÿ‡ฆ

King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

and more 2 locations

Natural History of Infantile Neuroaxonal Dystrophy

Completed
Conditions
INAD
Infantile Neuroaxonal Dystrophy
First Posted Date
2019-06-27
Last Posted Date
2020-06-29
Lead Sponsor
Retrotope, Inc.
Target Recruit Count
13
Registration Number
NCT03999814
Locations
๐Ÿ‡บ๐Ÿ‡ธ

Sarah Endemann, Los Altos, California, United States

A Study to Assess Efficacy and Safety of RT001 in Subjects With Infantile Neuroaxonal Dystrophy

Phase 2
Active, not recruiting
Conditions
Infantile Neuroaxonal Dystrophy
Interventions
First Posted Date
2018-06-27
Last Posted Date
2021-10-14
Lead Sponsor
Retrotope, Inc.
Target Recruit Count
19
Registration Number
NCT03570931
Locations
๐Ÿ‡บ๐Ÿ‡ธ

Jacobs Levy Genomics and Research Program, Morristown, New Jersey, United States

๐Ÿ‡บ๐Ÿ‡ธ

University of California San Francisco, Benioff Children's Hospital, San Francisco, California, United States

A First in Human Study of RT001 in Patients With Friedreich's Ataxia

Phase 1
Completed
Conditions
Friedreich's Ataxia
Interventions
Drug: Low dose cohort
Drug: High dose cohort
First Posted Date
2015-05-15
Last Posted Date
2020-11-27
Lead Sponsor
Retrotope, Inc.
Target Recruit Count
19
Registration Number
NCT02445794
Locations
๐Ÿ‡บ๐Ÿ‡ธ

Collaborative Neuroscience Network, LLC, Long Beach, California, United States

๐Ÿ‡บ๐Ÿ‡ธ

University of South Florida, Tampa, Florida, United States

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