Columbia University researchers report that ulefnersen, an experimental drug, demonstrated remarkable efficacy in treating FUS-ALS, a rare genetic form of ALS affecting young people.
The United Network for Organ Sharing's Composite Allocation Score implemented in March 2023 has dramatically reduced lung transplant waitlist mortality from 11.2% to 4.1%.
Recent research shows that ozone pollution exposure during a child's first two years increases asthma risk by 31% at ages 4-6, highlighting the need for long-term ozone regulation.
Research at the OncLive National Fellows Forum demonstrates UCHL1 inhibition shows promise as a therapeutic target in high-grade serous ovarian cancer, with varying effects based on chemotherapy resistance status.
A large-scale newborn genomic screening program in New York City demonstrated high parental consent rates, with 72% of approached families agreeing to participate.
A nationwide Phase 2A-2B clinical trial, named BenfoTeam, is underway to assess benfotiamine, a synthetic form of vitamin B1, for treating mild cognitive impairment and early Alzheimer's disease.