MedPath

Asklepios Biopharmaceutical, Inc.

Asklepios Biopharmaceutical, Inc. logo
🇺🇸United States
Ownership
Subsidiary
Established
2001-01-01
Employees
501
Market Cap
-
Website
http://www.askbio.com

Clinical Trials

6

Active:3
Completed:0

Trial Phases

2 Phases

Phase 1:3
Phase 2:2

Drug Approvals

0

Drug Approvals

No drug approvals found

This company may not have drug approvals in our database

Clinical Trials

Distribution across different clinical trial phases (5 trials with phase data)• Click on a phase to view related trials

Phase 1
3 (60.0%)
Phase 2
2 (40.0%)

A Study of AAV2-GDNF in Adults With Moderate Parkinson's Disease (REGENERATE-PD)

Phase 2
Recruiting
Conditions
Parkinson Disease
Interventions
Drug: AAV2-GDNF Gene therapy
Procedure: Control Surgery
First Posted Date
2024-02-29
Last Posted Date
2025-07-01
Lead Sponsor
AskBio Inc
Target Recruit Count
87
Registration Number
NCT06285643
Locations
🇺🇸

UCI Alpha Clinic (Neurology), Irvine, California, United States

🇺🇸

Loma Linda University (Neurology), Loma Linda, California, United States

🇺🇸

Loma Linda University (Surgical), Loma Linda, California, United States

and more 36 locations

Pre-Gene Therapy Study in Parkinson's Disease and Multiple System Atrophy

Active, not recruiting
Conditions
Multiple System Atrophy, Parkinson Variant
Parkinson's Disease
Multiple System Atrophy
First Posted Date
2023-01-26
Last Posted Date
2024-06-07
Lead Sponsor
Asklepios Biopharmaceutical, Inc.
Target Recruit Count
150
Registration Number
NCT05699460
Locations
🇺🇸

University of California Irvine, Irvine, California, United States

🇺🇸

Parkinson's Disease and Movement Disorders Center of Boca Raton, Boca Raton, Florida, United States

🇺🇸

Massachusetts General Hospital, Boston, Massachusetts, United States

and more 8 locations

Phosphatase Inhibition by Intracoronary Gene Therapy in Subjects With Non-Ischemic NYHA Class III Heart Failure

Phase 2
Recruiting
Conditions
Congestive Heart Failure
Interventions
First Posted Date
2022-10-28
Last Posted Date
2025-05-31
Lead Sponsor
AskBio Inc
Target Recruit Count
150
Registration Number
NCT05598333
Locations
🇺🇸

Cardiology P.C. Birmingham, Birmingham, Alabama, United States

🇺🇸

University of California San Diego, La Jolla, California, United States

🇺🇸

Baycare Medical Group, Clearwater, Florida, United States

and more 43 locations

A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)

Phase 1
Recruiting
Conditions
Muscular Dystrophy
Fukutin Related Protein
Limb-Girdle Muscular Dystrophy Type 2
LGMD2
LGMD
FKRP
FKRP Mutation
Limb Girdle Muscular Dystrophy
LGMD2I
First Posted Date
2022-02-09
Last Posted Date
2024-11-28
Lead Sponsor
Asklepios Biopharmaceutical, Inc.
Target Recruit Count
10
Registration Number
NCT05230459
Locations
🇺🇸

University of California - Irvine, Irvine, California, United States

🇺🇸

University of Iowa, Iowa City, Iowa, United States

🇺🇸

University of Kansas Medical Center, Kansas City, Kansas, United States

and more 3 locations

AB-1002 in Patients With Class III Heart Failure

Phase 1
Active, not recruiting
Conditions
Congestive Heart Failure
Heart Failure, Diastolic
Heart; Complications
Heart Disease, Ischemic
Heart Failure, Systolic
Heart Failure
Cardiovascular Diseases
Heart Failure,Congestive
Heart Arrhythmia
Interventions
Biological: 3 x 10e13vg AB-1002
First Posted Date
2019-11-27
Last Posted Date
2025-04-08
Lead Sponsor
AskBio Inc
Target Recruit Count
17
Registration Number
NCT04179643
Locations
🇺🇸

Minneapolis Heart Foundation Institute, Minneapolis, Minnesota, United States

🇺🇸

The Linder Center for Education and Research at The Christ Hospital, Cincinnati, Ohio, United States

🇺🇸

The Ohio State University, Columbus, Ohio, United States

and more 1 locations
  • Prev
  • 1
  • 2
  • Next

News

AskBio's AB-1003 Receives FDA Rare Pediatric Disease and Orphan Drug Designations for LGMD2I/R9

AskBio's AB-1003 (LION-101) has been granted rare pediatric disease designation by the FDA for limb-girdle muscular dystrophy type 2I/R9 (LGMD2I/R9).

© Copyright 2025. All Rights Reserved by MedPath