Rare Thyroid Therapeutics International AB
- Country
- πΈπͺSweden
- Ownership
- Subsidiary
- Established
- 2013-01-01
- Employees
- 1
- Market Cap
- -
- Website
- http://www.rarethyroid.com
Clinical Trials
12
Trial Phases
3 Phases
Drug Approvals
1
Drug Approvals
Clinical Trials
Distribution across different clinical trial phases (10 trials with phase data)β’ Click on a phase to view related trials
MCT8 Deficiency Caregiver Study
- Conditions
- Allan-Herndon-Dudley SyndromeMonocarboxylate Transporter 8 (MCT8) Deficiency
- First Posted Date
- 2023-09-29
- Last Posted Date
- 2024-04-25
- Lead Sponsor
- Rare Thyroid Therapeutics International AB
- Target Recruit Count
- 21
- Registration Number
- NCT06060197
- Locations
- π¬π§
Vitaccess Ltd, Oxford, Oxfordshire, United Kingdom
Expanded Access Program for Tiratricol in Patients With Monocarboxylate Transporter 8 Deficiency
- Conditions
- Monocarboxylate Transporter 8 DeficiencyAllan-Herndon-Dudley Syndrome
- First Posted Date
- 2023-06-22
- Last Posted Date
- 2025-09-24
- Lead Sponsor
- Rare Thyroid Therapeutics International AB
- Registration Number
- NCT05911399
- Locations
- πΊπΈ
University of Alabama at Birmingham Hospital, Birmingham, Alabama, United States
πΊπΈValley Children's Hospital, Madera, California, United States
πΊπΈRady Children's Hospital, San Diego, California, United States
Withdrawal of Tiratricol Treatment in Males with Monocarboxylate Transporter 8 Deficiency (MCT8 Deficiency)
- Conditions
- Allan-Herndon-Dudley SyndromeMonocarboxylate Transporter 8 Deficiency
- Interventions
- Drug: Placebo
- First Posted Date
- 2022-10-13
- Last Posted Date
- 2025-01-13
- Lead Sponsor
- Rare Thyroid Therapeutics International AB
- Target Recruit Count
- 16
- Registration Number
- NCT05579327
- Locations
- πΊπΈ
Rare Disease Research, LLC, Hillsborough, North Carolina, United States
πΊπΈSSM Health Cardinal Glennon Children's Hospital, Saint Louis, Missouri, United States
πΊπΈChildren's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Triac Trial II in MCT8 Deficiency Patients
- Conditions
- Allan-Herndon-Dudley Syndrome
- Interventions
- Drug: Triac
- First Posted Date
- 2015-03-24
- Last Posted Date
- 2024-12-19
- Lead Sponsor
- Rare Thyroid Therapeutics International AB
- Target Recruit Count
- 22
- Registration Number
- NCT02396459
- Locations
- πΊπΈ
Oregon Health & Science University (OHSU) Doernbecher Childrens Hospital, Portland, Oregon, United States
πΊπΈChildren's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
π¨πΏCharles University and Motol University Hospital; The department of peadiatrics of the 2nd faculty of medicine, Praha, Czechia