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Rare Thyroid Therapeutics International AB

Rare Thyroid Therapeutics International AB logo
🇸🇪Sweden
Ownership
Subsidiary
Established
2013-01-01
Employees
1
Market Cap
-
Website
http://www.rarethyroid.com

MCT8 Deficiency Caregiver Study

Completed
Conditions
Allan-Herndon-Dudley Syndrome
Monocarboxylate Transporter 8 (MCT8) Deficiency
First Posted Date
2023-09-29
Last Posted Date
2024-04-25
Lead Sponsor
Rare Thyroid Therapeutics International AB
Target Recruit Count
21
Registration Number
NCT06060197
Locations
🇬🇧

Vitaccess Ltd, Oxford, Oxfordshire, United Kingdom

Expanded Access Program for Tiratricol in Patients With Monocarboxylate Transporter 8 Deficiency

Conditions
Monocarboxylate Transporter 8 Deficiency
Allan-Herndon-Dudley Syndrome
First Posted Date
2023-06-22
Last Posted Date
2025-05-13
Lead Sponsor
Rare Thyroid Therapeutics International AB
Registration Number
NCT05911399
Locations
🇺🇸

University of Alabama at Birmingham Hospital, Birmingham, Alabama, United States

🇺🇸

Valley Children's Hospital, Madera, California, United States

🇺🇸

Rady Children's Hospital, San Diego, California, United States

and more 11 locations

Withdrawal of Tiratricol Treatment in Males with Monocarboxylate Transporter 8 Deficiency (MCT8 Deficiency)

Phase 3
Recruiting
Conditions
Allan-Herndon-Dudley Syndrome
Monocarboxylate Transporter 8 Deficiency
Interventions
Drug: Placebo
First Posted Date
2022-10-13
Last Posted Date
2025-01-13
Lead Sponsor
Rare Thyroid Therapeutics International AB
Target Recruit Count
16
Registration Number
NCT05579327
Locations
🇺🇸

Rare Disease Research, LLC, Hillsborough, North Carolina, United States

🇺🇸

SSM Health Cardinal Glennon Children's Hospital, Saint Louis, Missouri, United States

🇺🇸

Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States

and more 3 locations

Triac Trial II in MCT8 Deficiency Patients

Phase 2
Active, not recruiting
Conditions
Allan-Herndon-Dudley Syndrome
Interventions
Drug: Triac
First Posted Date
2015-03-24
Last Posted Date
2024-12-19
Lead Sponsor
Rare Thyroid Therapeutics International AB
Target Recruit Count
22
Registration Number
NCT02396459
Locations
🇳🇱

Erasmus MC, Rotterdam, Netherlands

🇺🇸

Oregon Health & Science University (OHSU) Doernbecher Childrens Hospital, Portland, Oregon, United States

🇩🇪

Charité - Universitätsmedizin Berlin Institut fur experimental paediatrische endokrinologie, Berlin, Germany

and more 2 locations
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