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Rare Thyroid Therapeutics International AB

Rare Thyroid Therapeutics International AB logo
πŸ‡ΈπŸ‡ͺSweden
Ownership
Subsidiary
Established
2013-01-01
Employees
1
Market Cap
-
Website
http://www.rarethyroid.com

Clinical Trials

12

Active:6
Completed:2

Trial Phases

3 Phases

Phase 1:5
Phase 2:3
Phase 3:2

Drug Approvals

1

EMA:1

Drug Approvals

Emcitate

Authorization Status
Authorised
Approval Date
Feb 12, 2025
EMA

Clinical Trials

Distribution across different clinical trial phases (10 trials with phase data)β€’ Click on a phase to view related trials

Phase 1
5 (50.0%)
Phase 2
3 (30.0%)
Phase 3
2 (20.0%)

MCT8 Deficiency Caregiver Study

Completed
Conditions
Allan-Herndon-Dudley Syndrome
Monocarboxylate Transporter 8 (MCT8) Deficiency
First Posted Date
2023-09-29
Last Posted Date
2024-04-25
Lead Sponsor
Rare Thyroid Therapeutics International AB
Target Recruit Count
21
Registration Number
NCT06060197
Locations
πŸ‡¬πŸ‡§

Vitaccess Ltd, Oxford, Oxfordshire, United Kingdom

Expanded Access Program for Tiratricol in Patients With Monocarboxylate Transporter 8 Deficiency

Conditions
Monocarboxylate Transporter 8 Deficiency
Allan-Herndon-Dudley Syndrome
First Posted Date
2023-06-22
Last Posted Date
2025-09-24
Lead Sponsor
Rare Thyroid Therapeutics International AB
Registration Number
NCT05911399
Locations
πŸ‡ΊπŸ‡Έ

University of Alabama at Birmingham Hospital, Birmingham, Alabama, United States

πŸ‡ΊπŸ‡Έ

Valley Children's Hospital, Madera, California, United States

πŸ‡ΊπŸ‡Έ

Rady Children's Hospital, San Diego, California, United States

and more 12 locations

Withdrawal of Tiratricol Treatment in Males with Monocarboxylate Transporter 8 Deficiency (MCT8 Deficiency)

Phase 3
Recruiting
Conditions
Allan-Herndon-Dudley Syndrome
Monocarboxylate Transporter 8 Deficiency
Interventions
Drug: Placebo
First Posted Date
2022-10-13
Last Posted Date
2025-01-13
Lead Sponsor
Rare Thyroid Therapeutics International AB
Target Recruit Count
16
Registration Number
NCT05579327
Locations
πŸ‡ΊπŸ‡Έ

Rare Disease Research, LLC, Hillsborough, North Carolina, United States

πŸ‡ΊπŸ‡Έ

SSM Health Cardinal Glennon Children's Hospital, Saint Louis, Missouri, United States

πŸ‡ΊπŸ‡Έ

Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States

and more 3 locations

Triac Trial II in MCT8 Deficiency Patients

Phase 2
Active, not recruiting
Conditions
Allan-Herndon-Dudley Syndrome
Interventions
Drug: Triac
First Posted Date
2015-03-24
Last Posted Date
2024-12-19
Lead Sponsor
Rare Thyroid Therapeutics International AB
Target Recruit Count
22
Registration Number
NCT02396459
Locations
πŸ‡ΊπŸ‡Έ

Oregon Health & Science University (OHSU) Doernbecher Childrens Hospital, Portland, Oregon, United States

πŸ‡ΊπŸ‡Έ

Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States

πŸ‡¨πŸ‡Ώ

Charles University and Motol University Hospital; The department of peadiatrics of the 2nd faculty of medicine, Praha, Czechia

and more 2 locations

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