Clinical Trials
3
Trial Phases
1 Phases
Drug Approvals
0
Drug Approvals
No drug approvals found
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Clinical Trials
Distribution across different clinical trial phases (2 trials with phase data)• Click on a phase to view related trials
VAL-1221 Delivered Intravenously in Ambulatory and Ventilator-free Participants With Late-Onset Pompe Disease
- First Posted Date
- 2016-09-13
- Last Posted Date
- 2020-06-02
- Lead Sponsor
- Valerion Therapeutics, LLC
- Target Recruit Count
- 12
- Registration Number
- NCT02898753
- Locations
- 🇺🇸
University of California, Irvine, Orange, California, United States
🇺🇸Duke University Medical Center, Durham, North Carolina, United States
🇬🇧National Hospital for Neurology and Neurosurgery, London, United Kingdom
Prospective, Longitudinal Study of the Natural History and Functional Status of Patients With Myotubular Myopathy (MTM)
- Conditions
- Myotubular Myopathy
- First Posted Date
- 2014-02-07
- Last Posted Date
- 2018-06-07
- Lead Sponsor
- Valerion Therapeutics, LLC
- Target Recruit Count
- 48
- Registration Number
- NCT02057705
- Locations
- 🇺🇸
Boston Children's Hospital, 300 Longwood Avenue, Boston, Massachusetts, United States
🇧🇪Centre Hospitalier Regional de la Citadelle, Liège, Belgium
🇨🇦Hospital for Sick Children, 555 University Avenue, Toronto, Ontario, Canada