MedPath

TREATMENTS FOR EPILEPSY AND SYMPTOMS OF SLC13A5 FOUNDATION

🇺🇸United States
Ownership
-
Employees
-
Market Cap
-
Website

Clinical Trials

3

Active:0
Completed:0

Trial Phases

1 Phases

Not Applicable:1

Drug Approvals

0

Drug Approvals

No drug approvals found

This company may not have drug approvals in our database

Clinical Trials

Distribution across different clinical trial phases (1 trials with phase data)• Click on a phase to view related trials

Not Applicable
1 (100.0%)

Intrathecal Gene Therapy For SLC13A5 Citrate Transporter Disorder

Not Applicable
Not yet recruiting
Conditions
SLC13A5 Citrate Transporter Disorder
Interventions
First Posted Date
2025-08-03
Last Posted Date
2025-08-14
Lead Sponsor
TESS Research Foundation
Target Recruit Count
2
Registration Number
NCT07102524
Locations
🇺🇸

University of Texas Southwestern Medical Center, Dallas, Texas, United States

SLC13A5 Deficiency Natural History Study - United States Only

Conditions
Citrate Transporter Deficiency
Epilepsy
Rare Diseases
Movement Disorders
Genetic Disorder
SLC13A5 Deficiency
EIEE25
Kohlschutter-Tonz Syndrome (Non-ROGDI)
Citrate Transporter Disorder
DEE25
First Posted Date
2023-11-22
Last Posted Date
2025-08-05
Lead Sponsor
TESS Research Foundation
Target Recruit Count
17
Registration Number
NCT06144957
Locations
🇺🇸

Lucille Packard Children's Hospital, Stanford University, Palo Alto, California, United States

🇺🇸

Brown University, Providence, Rhode Island, United States

🇺🇸

University of Texas Southwestern Dallas, Dallas, Texas, United States

SLC13A5 Deficiency Natural History Study - Remote Only

Conditions
Citrate Transporter Deficiency
Epilepsy
Rare Diseases
Movement Disorders
Genetic Disorder
SLC13A5 Deficiency
EIEE25
Kohlschutter-Tonz Syndrome (non-ROGDI)
17p13.1 Deletions Confined to SLC13A5 Gene
Citrate Transporter Disorder
First Posted Date
2020-12-23
Last Posted Date
2024-11-22
Lead Sponsor
TESS Research Foundation
Target Recruit Count
20
Registration Number
NCT04681781
Locations
🇺🇸

Lucille Packard Children's Hospital, Stanford University, Palo Alto, California, United States

News

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