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Mirum Pharmaceuticals

Mirum Pharmaceuticals logo
🇺🇸United States
Ownership
Public
Established
2018-01-01
Employees
264
Market Cap
$2.1B
Website
http://www.mirumpharma.com
Introduction

Mirum Pharmaceuticals, Inc. is a biopharmaceutical company. The firm focuses on the development and commercialization of a late-stage pipeline of novel therapies for debilitating liver diseases. Its products include Maralixibat and Volixibat. The company was founded by Niall O'Donnel, Michael Grey and Christopher Peetz in May 2018 and is headquartered in Foster City, CA.

Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid

Phase 3
Completed
Conditions
Zellweger Syndrome
Cholestasis
Infantile Refsum's Disease
Adrenoleukodystrophy
Peroxisomal Disorders
Interventions
Drug: Cholic Acids
First Posted Date
2000-12-07
Last Posted Date
2023-10-03
Lead Sponsor
Mirum Pharmaceuticals, Inc.
Target Recruit Count
85
Registration Number
NCT00007020
Locations
🇺🇸

Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States

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