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Ocugen

Ocugen logo
🇺🇸United States
Ownership
Public
Established
2013-01-01
Employees
65
Market Cap
$382.8M
Website
http://www.ocugen.com
Introduction

Ocugen, Inc. is a biopharmaceutical company, which engages in the development and commercialization of therapies to cure eye diseases. Its product pipeline candidates include OCU400, OCU410, OCU200, and COVAXIN. The firm's modifier gene therapy platform is engaged in addressing retinal diseases, including retinitis pigmentosa, leber congenital amaurosis, and dry age-related macular degeneration. The company was founded by Shankar Musunuri and Uday B. Kompella in 2013 and is headquartered in Malvern, PA.

Clinical Trials

11

Active:2
Completed:2

Trial Phases

4 Phases

Phase 1:3
Phase 2:2
Phase 3:3
+1 more phases

Drug Approvals

0

Drug Approvals

No drug approvals found

This company may not have drug approvals in our database

Clinical Trials

Distribution across different clinical trial phases (9 trials with phase data)• Click on a phase to view related trials

Phase 1
3 (33.3%)
Phase 3
3 (33.3%)
Phase 2
2 (22.2%)
Not Applicable
1 (11.1%)

Expanded Access Program for RP in Adults

Conditions
Retinitis Pigmentosa
First Posted Date
2024-08-28
Last Posted Date
2025-07-28
Lead Sponsor
Ocugen
Registration Number
NCT06574997
Locations
🇺🇸

Associated Retina Consultants, Phoenix, Arizona, United States

🇺🇸

Advanced Research, Deerfield Beach, Florida, United States

🇺🇸

Erie Retina Research, Erie, Pennsylvania, United States

and more 1 locations

A Phase 3 Study Of OCU400 Gene Therapy for the Treatment Of Retinitis Pigmentosa

Phase 3
Recruiting
Conditions
Retinitis Pigmentosa
First Posted Date
2024-04-29
Last Posted Date
2025-08-03
Lead Sponsor
Ocugen
Target Recruit Count
150
Registration Number
NCT06388200
Locations
🇨🇦

Research Institute of the McGill University Health Centre, Montréal, Quebec, Canada

🇺🇸

Associated Retina Consultants, Phoenix, Arizona, United States

🇺🇸

University of Southern Califormia, La Jolla, California, United States

and more 14 locations

Study to Assess the Safety and Efficacy of OCU410 for Geographic Atrophy

Phase 1
Active, not recruiting
Conditions
Geographic Atrophy
First Posted Date
2023-08-30
Last Posted Date
2025-06-17
Lead Sponsor
Ocugen
Target Recruit Count
60
Registration Number
NCT06018558
Locations
🇺🇸

Advanced Research, LLC, Coral Springs, Florida, United States

🇺🇸

The Retina Institute, Saint Louis, Missouri, United States

🇺🇸

Valley retina Institute, McAllen, Texas, United States

and more 9 locations

A Phase 2/3 Trial to Assess the Efficacy and Safety of OCU410ST for Stargardt Disease

Not Applicable
Recruiting
Conditions
Stargardt Disease
Interventions
First Posted Date
2023-07-21
Last Posted Date
2025-07-29
Lead Sponsor
Ocugen
Target Recruit Count
51
Registration Number
NCT05956626
Locations
🇺🇸

Vitreo Retinal Associates, P.A., Gainesville, Florida, United States

🇺🇸

Advanced Research, LLC, Pompano Beach, Florida, United States

🇺🇸

Retina Partners Midwest, P.C., Carmel, Indiana, United States

and more 10 locations

Phase I Study to Assess the Safety and Efficacy of OCU200 for Center-Involved Diabetic Macular Edema (DME)

Phase 1
Recruiting
Conditions
Center Involved Diabetic Macular Edema
Diabetic Macular Edema
Interventions
First Posted Date
2023-04-06
Last Posted Date
2025-08-06
Lead Sponsor
Ocugen
Target Recruit Count
30
Registration Number
NCT05802329
Locations
🇺🇸

Advanced Research LLC, Deerfield Beach, Florida, United States

🇺🇸

Erie Retina Research, LLC, Erie, Pennsylvania, United States

🇺🇸

Retina Consultants of Texas Research Centers, Bellaire, Texas, United States

and more 2 locations
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News

Stargardt Disease Pipeline Shows Promising Progress with Multiple Gene Therapies Advancing to Late-Stage Trials

Ocugen's OCU410ST gene therapy has received FDA approval to launch a Phase 2/3 pivotal confirmatory trial for treating all forms of Stargardt disease, with the potential to serve as the foundation for a biologics license application.

Carisma Therapeutics and OrthoCellix Announce $25M Merger to Advance Phase 3 Knee Cartilage Therapy

Carisma Therapeutics and OrthoCellix have entered into a definitive merger agreement to create a Nasdaq-listed regenerative cell therapy company focused on orthopedic diseases.

Ocugen Secures $161M Gene Therapy Licensing Deal for OCU400 in Korean Market

Ocugen signed a binding term sheet with a Korean pharmaceutical leader for exclusive rights to OCU400, a novel modifier gene therapy for retinitis pigmentosa, potentially worth over $161 million.

OCU410 Gene Therapy Shows Promise for Geographic Atrophy with Single-Dose Treatment Approach

OCU410 gene therapy demonstrated a 21.4% reduction in geographic atrophy lesion growth in low-dose patients after 6 months compared to untreated fellow eyes.

Three Pharmaceutical Companies Advance Next-Generation COVID-19 Therapeutics in Clinical Trials

INOVIO Pharmaceuticals reports promising Phase I results for its DMAbs technology, showing 100% of subjects maintained relevant antibody levels with no serious adverse events.

Opthia Faces $1 Billion Investor Obligation Following Sozinibercept Trial Failure in WetAMD

Opthia may owe up to $1 billion to investors following the failure of sozinibercept in clinical trials for wet age-related macular degeneration (WetAMD).

WashU's Novel Nasal COVID-19 Vaccine Advances to U.S. Phase 1 Clinical Trials

FDA approves Ocugen's investigational new drug application for a nasal COVID-19 vaccine, developed at Washington University in St. Louis, advancing to Phase 1 clinical trials this spring.

Ocugen's Inhaled COVID-19 Vaccine Candidate, OCU500, Advances to Phase 1 Trial After FDA Review

Ocugen's OCU500, a novel inhaled mucosal vaccine for COVID-19, has received IND clearance from the FDA, allowing a Phase 1 clinical trial to proceed.

Dry AMD Therapeutic Pipeline Shows Promise with 70+ Companies Advancing Novel Therapies

The dry age-related macular degeneration (AMD) therapeutic landscape is robust, with over 70 companies developing more than 80 therapies.

Ocugen Doses First Patient in Phase 1 Trial of OCU200 for Diabetic Macular Edema

Ocugen has initiated a Phase 1 clinical trial for OCU200, a novel integrin-targeting biologic, in patients with diabetic macular edema (DME).

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