FONDAZIONE TELETHON ETS
- Country
- ๐ฎ๐นItaly
- Ownership
- Subsidiary
- Established
- 1990-01-01
- Employees
- 51
- Market Cap
- -
- Website
- http://telethon.it
Methodology Study of Retroviral Insertion Site Analysis in Strimvelis Gene Therapy
- Conditions
- Interventions
- First Posted Date
- 2021-07-13
- Last Posted Date
- 2024-01-29
- Lead Sponsor
- Fondazione Telethon
- Target Recruit Count
- 15
- Registration Number
- NCT04959890
- Locations
- ๐ฎ๐น
Ospedale San Raffaele, Milan, Italy
A Clinical Study to Evaluate the Use of a Cryopreserved Formulation of OTL-103 in Subjects With Wiskott-Aldrich Syndrome
- First Posted Date
- 2019-02-12
- Last Posted Date
- 2024-01-31
- Lead Sponsor
- Fondazione Telethon
- Target Recruit Count
- 10
- Registration Number
- NCT03837483
- Locations
- ๐ฎ๐น
Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET), Milan, Italy
๐บ๐ธChildren's Healthcare of Atlanta, Inc, Atlanta, Georgia, United States
Natural History Study in Subjects With Usher Syndrome
- Conditions
- First Posted Date
- 2019-01-24
- Last Posted Date
- 2024-12-09
- Lead Sponsor
- Fondazione Telethon
- Target Recruit Count
- 56
- Registration Number
- NCT03814499
- Locations
- ๐ฎ๐น
Eye Clinic of the University of Campania Luigi Vanvitelli, Naples, Italy
๐ณ๐ฑStichting Oogziekenhuis Rotterdam, Rotterdam, Netherlands
๐ช๐ธInstituto de Investigacion Sanitaria de la Fundacion Jimenez Diaz, Madrid, Spain
Use of Phenylbutyrate Therapy for Patients With Pyruvate Dehydrogenase Complex Deficiency.
- Conditions
- Interventions
- First Posted Date
- 2018-11-07
- Last Posted Date
- 2021-10-13
- Lead Sponsor
- Fondazione Telethon
- Target Recruit Count
- 1
- Registration Number
- NCT03734263
- Locations
- ๐ฎ๐น
Federico II University, Napoli, Italy
Strimvelis Registry Study to Follow-up Patients With Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID)
- Conditions
- Interventions
- First Posted Date
- 2018-03-27
- Last Posted Date
- 2024-01-29
- Lead Sponsor
- Fondazione Telethon
- Target Recruit Count
- 50
- Registration Number
- NCT03478670
- Locations
- ๐ฎ๐น
Ospedale San Raffaele, Milano, Lombardia, Italy
Retroviral Insertion Site Methodology Study
- First Posted Date
- 2017-10-16
- Last Posted Date
- 2024-01-29
- Lead Sponsor
- Fondazione Telethon
- Registration Number
- NCT03311074
Evaluating the Effectiveness of STRIMVELIS Risk Minimization Measures (RMMs)
- Conditions
- Interventions
- First Posted Date
- 2017-07-27
- Last Posted Date
- 2023-11-14
- Lead Sponsor
- Fondazione Telethon
- Target Recruit Count
- 16
- Registration Number
- NCT03232203
- Locations
- ๐ฎ๐น
Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET), Milan, Italy
Gene Therapy in Patients With Mucopolysaccharidosis Disease
- First Posted Date
- 2017-06-02
- Last Posted Date
- 2024-11-22
- Lead Sponsor
- Fondazione Telethon
- Target Recruit Count
- 9
- Registration Number
- NCT03173521
- Locations
- ๐น๐ท
Children's Hospital Hacettepe University, Ankara, Turkey
๐ฎ๐นDepartment of Translational Medicine (DISMET) of "Federico II" University, Naples, Naples, Italy
Gene Therapy for Wiskott-Aldrich Syndrome
- First Posted Date
- 2012-01-24
- Last Posted Date
- 2024-01-31
- Lead Sponsor
- Fondazione Telethon
- Target Recruit Count
- 8
- Registration Number
- NCT01515462
- Locations
- ๐ฎ๐น
Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET), Milan, Italy
ADA Gene Transfer Into Hematopoietic Stem/Progenitor Cells for the Treatment of ADA-SCID
- Conditions
- Interventions
- First Posted Date
- 2008-01-22
- Last Posted Date
- 2024-01-29
- Lead Sponsor
- Fondazione Telethon
- Target Recruit Count
- 12
- Registration Number
- NCT00598481
- Locations
- ๐ฎ๐ฑ
Investigational Site, Jerusalem, Israel
๐ฎ๐นOspedale San Raffaele, Milano, Lombardia, Italy