Ketogenic Diet in Lafora Disease

计划入组 15 人 · 首次发布于 2000 年 12 月 8 日

Natural History and Functional Status Study of Patients With Lafora Disease

计划入组 33 人 · 首次发布于 2019 年 3 月 15 日

A Safety and Efficacy of Intrathecally Administered ION283 in Patients With Lafora Disease

计划入组 10 人 · 首次发布于 2024 年 9 月 24 日

ION-648402

liver disease program

siRNA therapeutics for ocular disease/dermatological disease (Phio Pharmaceuticals)

Rare Disease Research, LLC

CASTLEMAN DISEASE COLLABORATIVE NETWORK

United States

CURE RARE DISEASE, INC.

United States

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