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找到 17,161 条关于
“alpha-thalassemia major”
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17,161
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7,411
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上个月
Hong Kong Establishes First PIC/S GMP-Certified Stem Cell Manufacturing Facility, Advancing Cell and Gene Therapy Ecosystem
去年
Gene Therapy Demonstrates Promise as One-Time Treatment for Alpha Thalassemia
去年
Agios' Pyrukynd Faces FDA Decision for Thalassemia Treatment by September 2025
去年
Mitapivat Shows Promise in Phase 3 Trial for Transfusion-Dependent Thalassemia
去年
Chinese Base Editing Therapy Successfully Cures Thalassemia in Four Children
去年
Agios' Mitapivat Receives Positive CHMP Opinion for Thalassemia Treatment in Europe
9个月前
FDA Extends Review Timeline for Agios' Mitapivat Thalassemia Application Beyond PDUFA Date
去年
Alpha Tau Secures MDSAP Certification for Alpha DaRT Cancer Therapy Manufacturing Facility
6年前
Gene Therapy Shows Promise in Treating Severe β-Thalassemia
去年
Agios Pharmaceuticals Faces FDA Delay for Pyrukynd Thalassemia Approval Amid Safety Concerns
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