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找到 551 条关于
“thalassaemia”
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551
临床试验
511
药物
8
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32
2年前
Chinese Base Editing Therapy Achieves First Clinical Cure of Beta Thalassaemia
2年前
NHS England Approves First CRISPR Gene-Editing Therapy for Beta Thalassaemia Treatment
8个月前
NHS Patient Achieves Transfusion Independence Following CRISPR Gene Therapy for Beta Thalassaemia
5个月前
Transformer Base Editor Shows Promise in First Clinical Trial for β-Thalassaemia Treatment
27天前
Doctors Achieve Landmark Recoveries with Haplo-Cord Transplant and Dual-Target CAR T-Cell Therapy
6年前
Gene Therapy Shows Promise in Treating Severe β-Thalassemia
去年
Chinese Base Editing Therapy Successfully Cures Thalassemia in Four Children
去年
Gene Therapy Demonstrates Promise as One-Time Treatment for Alpha Thalassemia
去年
Agios' Mitapivat Receives Positive CHMP Opinion for Thalassemia Treatment in Europe
去年
EMA Approves Bluebird Bio's Zynteglo, First Gene Therapy for Beta Thalassemia
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