NCT02018302No Longer Available不适用
Post Study Continuation of C7 for G1D
Juan Pascual1 个研究点 分布在 1 个国家开始时间: 2013年12月23日最近更新:
适应症
相关药物
试验速览
- 阶段
- 不适用
- 状态
- No Longer Available
- 发起方
- 试验地点
- 1
研究概览
简要总结
This protocol provides ongoing access to triheptanoin for patients who did complete an initial pilot protocol, and provides the opportunity to collect long-term safety data from patients treated with triheptanoin.
详细描述
Only patients who completed the initial pilot study were eligible. The study is ongoing with these patients only.
研究设计
- 研究类型
- Expanded Access
入排标准
- 年龄范围
- 1 Month 至 28 Years（Child, Adult）
- 性别
- All
- 接受健康志愿者
- 否
入选标准
- •Patients enrolled in the pilot trial (UTSW 122010-186)
排除标准
- •Subjects who did not complete the pilot trial (UTSW 122010-186)
研究者
Juan Pascual
Associate Professor, Director of the Rare Brain Disorders Program
University of Texas Southwestern Medical Center
研究点 (1)
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