NL-OMON39538尚未招募不适用
A Prospective Natural History Study of the Progression of Physical Impairment, Activity Limitation and Quality of Life in Duchenne Muscular Dystrophy (DMD) - DMD Natural History
Prosensa Therapeutics B.V.0 个研究点目标入组 30 人开始时间: 待定最近更新:
适应症
试验速览
- 阶段
- 不适用
- 状态
- 尚未招募
- 发起方
- 入组人数
- 30
研究概览
简要总结
暂无简介。
研究设计
- 研究类型
- Observational
入排标准
- 年龄范围
- 2 至 17（—）
入选标准
- •Diagnosis of DMD resulting from a mutation in the DMD gene confirmed by a state of the art DNA diagnostic technique covering all DMD gene exons.
- •Age 3 - 18 years
- •Willing and able to comply with protocol requirements
- •Life expectancy of at least 3 years
- •Able to give informed assent and/or consent in writing signed by the subject and/or parent(s)/legal guardian (according to local regulations)
排除标准
- •Current participation in a clinical study with an Investigational Medicinal Product(IMP)
- •Participation within the previous 1 month in a clinical study with an IMP
研究者
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