跳至主要内容
临床试验/NL-OMON35077
NL-OMON35077尚未招募不适用

Efficacy of dietary suppletion genestein in patients with the MPS III (A follow-up study) - Follow-up study genestein in MPS III

Academisch Medisch Centrum0 个研究点目标入组 30 人开始时间: 待定最近更新:
适应症

试验速览

阶段
不适用
状态
尚未招募
入组人数
30

研究概览

简要总结

暂无简介。

研究设计

研究类型
Interventional

入排标准

年龄范围
2 至 99(—)

入选标准

  • The patient should have a biochemically confirmed deficiency of heparan-N-Sulphatase (MPS IIIA) or A-N-acetylglucosaminidase (MPS IIIB) or Acetyl CoA: alpha-glucosaminide N-acetyltransefrase (MPS IIIC). All patients who participated in the placebo controlled cross-over trial with genestein are allowed to participate in this study.

排除标准

  • The parent/legal reprensentative is unwilling to participate
  • Patient underwent umbilical cord blood cell transplantation

研究者

相似试验