TREMOR IN CHARCOT-MARIE-TOOTH

计划入组 75 人 · 首次发布于 2026 年 5 月 6 日

Ulipristal Acetate In Disease Charcot-Marie-Tooth Type of 1A

计划入组 23 人 · 首次发布于 2015 年 11 月 9 日

Natural History Study for Charcot Marie Tooth Disease

计划入组 10,000 人 · 首次发布于 2023 年 6 月 15 日

Charcot-Marie-Tooth Disease Type 1A(Metagenomi)

Charcot Marie Tooth -Type 2A (MitoRx Therapeutics)

Beclin activator peripheral (Charcot Marie Tooth disease type 1A)

CHAS MARIE

France

MARIE CURIE

United Kingdom

FICHOT MARIE

France

Actio Biosciences Raises $66M Series B to Advance Rare Disease Programs Targeting Ion Channel Disorders

Jazz Pharmaceuticals to Acquire Actio Biosciences for $820 Million, Securing First-in-Class KCNT1 Epilepsy Therapy ABS-1230

Actio Biosciences Advances Precision Medicine Platform for Rare and Common Diseases