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找到 1,337 条关于
“GM2 gangliosidoses”
全部
1,337
临床试验
958
药物
280
机构
7
资讯
92
上个月
Andelyn Biosciences Partners with Queen's University to Manufacture AAV9-GM2 Gene Therapy for GM2 Gangliosidoses
3个月前
Azafaros Publishes Phase 2 RAINBOW Study Data for Nizubaglustat in GM2 Gangliosidosis and Niemann-Pick Type C Disease
去年
Azafaros' Nizubaglustat Gains Orphan Drug Designations, Phase 3 Trials to Start in 2025
7个月前
Azafaros to Present Phase 3 Nizubaglustat Data for Rare Lysosomal Storage Disorders at WORLDSymposium 2026
去年
Azafaros to Present at J.P. Morgan's 43rd Annual Healthcare Conference
去年
Azafaros Secures €130M Funding to Advance Nizubaglustat into Phase III for Rare Lysosomal Storage Disorders
去年
Azafaros Secures €132M Series B Financing to Advance Rare Lysosomal Storage Disorder Treatments
去年
MEDIPAL Holdings and JCR Pharmaceuticals Partner on Novel GM2 Gangliosidosis Therapy JR-479
去年
UMass Chan Gene Therapy Shows Biochemical Correction in GM2 Gangliosidosis Phase I/II Trial
去年
Efgartigimod Shows Promise in Treating Rare Neurological Autoimmune Disorders Beyond Myasthenia Gravis
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