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找到 1,336 条关于
“GM2 gangliosidosis”
全部
1,336
临床试验
954
药物
280
机构
7
资讯
95
去年
MEDIPAL Holdings and JCR Pharmaceuticals Partner on Novel GM2 Gangliosidosis Therapy JR-479
去年
UMass Chan Gene Therapy Shows Biochemical Correction in GM2 Gangliosidosis Phase I/II Trial
3个月前
Azafaros Publishes Phase 2 RAINBOW Study Data for Nizubaglustat in GM2 Gangliosidosis and Niemann-Pick Type C Disease
7个月前
Azafaros to Present Phase 3 Nizubaglustat Data for Rare Lysosomal Storage Disorders at WORLDSymposium 2026
去年
Azafaros to Present at J.P. Morgan's 43rd Annual Healthcare Conference
上个月
Andelyn Biosciences Partners with Queen's University to Manufacture AAV9-GM2 Gene Therapy for GM2 Gangliosidoses
去年
Azafaros Secures €130M Funding to Advance Nizubaglustat into Phase III for Rare Lysosomal Storage Disorders
去年
Azafaros' Nizubaglustat Gains Orphan Drug Designations, Phase 3 Trials to Start in 2025
上个月
In Utero Gene Therapy Trial Targets GM1 Gangliosidosis Before Birth
去年
Azafaros Secures €132M Series B Financing to Advance Rare Lysosomal Storage Disorder Treatments
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