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找到 36,319 条关于
“Hunter Syndrome”
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36,319
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6年前
Advancements in Neurology: From Hunter Syndrome to Alzheimer's Disease
去年
GC Biopharma's Hunterase ICV Approved in Russia for Severe Hunter Syndrome
去年
GC Biopharma's Hunterase Shows Significant Efficacy in Phase 3 Trial for Hunter Syndrome
去年
Revolutionary Gene Therapy and BBB-Penetrating Treatments Transform Hunter Syndrome Treatment Landscape
2年前
FDA Extends Review Timeline for REGENXBIO's Hunter Syndrome Gene Therapy RGX-121
去年
Denali Therapeutics' Tividenofusp Alfa Receives FDA Breakthrough Therapy Designation for Hunter Syndrome
7年前
Denali's Hunter Syndrome Candidate Receives FDA Orphan Drug and Rare Pediatric Disease Designations
9个月前
Denali Therapeutics Secures $275 Million Royalty Deal with Royalty Pharma for Hunter Syndrome Therapy
去年
JCR Pharmaceuticals Completes Enrollment in Global Phase III Trial for Blood-Brain Barrier-Penetrating Hunter Syndrome Therapy
9个月前
World-First Gene Therapy Shows Remarkable Success in Three-Year-Old with Hunter Syndrome
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