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找到 15,722 条关于
“Leber's congenital amaurosis 10”
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6年前
Free Genetic Testing Initiative Accelerates Drug Development for Inherited Retinal Diseases
4个月前
Six-Year-Old Girl Regains Vision Through Groundbreaking NHS Gene Therapy for Leber's Congenital Amaurosis
6年前
First In Vivo CRISPR Therapy Dosed in Clinical Trial for Congenital Blindness
去年
Variant Secures EMA Endorsement for VAR002 Gene Therapy Targeting Inherited Retinal Dystrophies
2年前
CRISPR Gene Editing Shows Promise in Treating Rare Form of Blindness
去年
HuidaGene's CRISPR/Cas13 RNA-Editing Therapy HG202 Cleared for US Trial in Macular Degeneration
9个月前
Rezolute's Ersodetug Fails Phase 3 Trial for Congenital Hyperinsulinism, Stock Plunges 88%
去年
FDA Approves Neurocrine's Crenessity (crinecerfont) for Congenital Adrenal Hyperplasia
5个月前
Philadelphia Scientists Win $3 Million Breakthrough Prize for First FDA-Approved Gene Therapy for Inherited Blindness
去年
Ocugen to Highlight Retinal Gene Therapy Progress at Clinical Showcase
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