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找到 4,012 条关于
“mutated enzyme”
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4,012
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1,685
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236
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20
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10个月前
FDA Investigates Fatal Adverse Event Linked to Takeda's Adzynma Enzyme Replacement Therapy
5个月前
Abbott Completes $21 Billion Exact Sciences Acquisition While Novartis Invests $2 Billion in Next-Generation PI3Kα Inhibitors
去年
Tibsovo Listed on Australian PBS, Offering First Targeted Therapy for Rare Bile Duct Cancer
6个月前
Novartis Acquires Next-Generation PI3Kα Inhibitor SNV4818 in $3 Billion Deal to Strengthen Breast Cancer Pipeline
去年
Health Canada Approves Vorasidenib (Voranigo) as First Targeted Therapy for IDH-Mutant Glioma
去年
Nine-Year-Old Becomes Third Patient Worldwide to Receive Experimental Gene Therapy for Rare Batten Disease
去年
FDA Approves Kebilidi, First Gene Therapy Directly Administered to the Brain for AADC Deficiency
去年
Chiesi's ELFABRIO Shows Promise in Phase 3 Trial for Fabry Disease with Twice-Dose Regimen
去年
EZH2 Inhibitors Enhance Lymphoma Immunotherapy in Preclinical Models
去年
BioMarin Acquires Inozyme Pharma for $270 Million, Adding Late-Stage Enzyme Therapy for Rare Genetic Disorder
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