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找到 79,046 条关于
“myotonic dystrophy type-1”
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79,046
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2个月前
Myotonia May Amplify Muscle Damage in Myotonic Dystrophy Type 1, New Study Reveals
10个月前
PepGen Secures U.S. Patent for PGN-EDODM1, Advancing Myotonic Dystrophy Type 1 Treatment
2年前
Avidity's Delpacibart Etedesiran Granted FDA Breakthrough Therapy Designation for Myotonic Dystrophy Type 1
8个月前
Experimental Compound Shows Promise for Myotonic Dystrophy Type 1 Treatment, Advances to Clinical Trial
去年
Japan Grants First Orphan Drug Designation for Myotonic Dystrophy Type 1 to Avidity's Del-desiran
11个月前
Sarepta Advances SRP-1003 siRNA Therapy for Myotonic Dystrophy Type 1 with Positive Safety Review
6个月前
ARTHEx Biotech Receives FDA Fast Track Designation for ATX-01 in Myotonic Dystrophy Type 1
11个月前
Dyne Therapeutics Reports Sustained One-Year Functional Improvements with Zeleciment Basivarsen in Myotonic Dystrophy Type 1
去年
ARTHEx Biotech Secures $87M Series B to Advance Novel RNA Therapy for Myotonic Dystrophy Type 1
7个月前
Avidity's Del-desiran Shows Promise for Myotonic Dystrophy Type 1 in Phase 1/2 MARINA Trial Published in NEJM
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