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找到 3,385 条关于
“phenylalanine hydroxylase (PAH)”
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3,385
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2,295
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526
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60
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504
去年
FDA Accepts PTC Therapeutics' NDA for Sepiapterin to Treat PKU
去年
FDA Accepts NDA for PTC Therapeutics' Sepiapterin in Phenylketonuria Treatment
去年
BioMarin Reports Positive Phase 3 Results for PALYNZIQ in Adolescent PKU Patients
9个月前
PTC Therapeutics Secures Global Approvals for Sephience in PKU Treatment Across Canada and Japan
去年
Phenylketonuria Pipeline Shows Robust Growth with 25+ Therapies in Development
去年
FDA Sets Q3 2025 Approval Dates for Three Breakthrough Therapies Targeting Rare Diseases
3个月前
Beam Therapeutics Receives FDA Clearance for BEAM-304, a First-in-Class In Vivo Base Editing Therapy for Phenylketonuria
25天前
PTC Therapeutics' Sephience (sepiapterin) Data Reinforce Broad PKU Benefits, Including Diet Liberalization and Sustained Metabolic Control
去年
BioMarin's Palynziq Shows Promising Results in Adolescents with PKU, Setting Stage for Label Expansion
去年
PTC Therapeutics' Sephience Receives Positive CHMP Opinion for Phenylketonuria Treatment Across All Age Groups
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