Cholesterol and Antioxidant Treatment in Patients With Smith-Lemli-Opitz Syndrome (SLOS)

计划入组 100 人 · 首次发布于 2013 年 1 月 23 日

Study of Smith-Lemli-Opitz Syndrome

计划入组 130 人 · 首次发布于 1999 年 11 月 4 日

Phase II Study of Cholesterol- and Cholestanol-Free Diet, Lovastatin, and Chenodeoxycholic Acid for Cerebrotendinous Xanthomatosis

计划入组 5 人 · 首次发布于 1999 年 10 月 19 日

Cholesterol

C₂₇H₄₆O

Cholesterol sulfate

C₂₇H₄₆O₄S

cholesterol targeting therapeutic

Free University of Brussels

Mary Free Bed Rehabilitation Hospital

United States

Royal Free NHS Foundation Trust

United Kingdom

FDA Grants Rare Disease Evidence Principles Eligibility to Repair Biotechnologies' mRNA Therapy for Homozygous Familial Hypercholesterolemia

AGC Biologics Partners with Repair Biotechnologies to Develop Novel mRNA Therapy for Atherosclerotic Cardiovascular Disease

FDA Grants Orphan Drug Designation to Repair Biotechnologies' mRNA Therapy for Rare Cholesterol Disorder