Transthyretin Amyloidosis Therapy (HuidaGene)

TTR gene therapy (transthyretin amyloidosis)

CRISPR-Cas12 gene therapy (HG-PRECISE, Transthyretin Amyloidosis)

amyloidosis therapy, orphanbiotec

cardiac selective mineralocorticoid receptor inhibitors (oral, cardiac failure/cardiac fibrosis)

Cardiac Fibrosis(Hepion)

Systemic amyloidosis (Illimis Therapeutics)

TTR gene editing therapy (Trucode Gene)

Tafamidis(Vyndamax, Vyndaqel)

C₁₄H₇Cl₂NO₃ · Rx

Patisiran(Onpattro)

Rx