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Study of Aripiprazole in the Treatment of Children and Adolescents With Autistic Disorder (AD)

Phase 3
Completed
Conditions
Behavioral Symptoms
Autistic Disorder
Interventions
Drug: Placebo
Registration Number
NCT00337571
Lead Sponsor
Otsuka Pharmaceutical Development & Commercialization, Inc.
Brief Summary

This study will compare the effectiveness (how well the drug works) of aripiprazole with placebo (fixed dose) in reducing serious behavioral problems in children and adolescents with a diagnosis of autistic disorder (AD).

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
218
Inclusion Criteria
  • Meets current Diagnostic and Statistical Manual of Mental Disorders, Fourth Edition, Text Revision (DSM-IV-TR) diagnostic criteria for AD and demonstrates serious behavioral problems; diagnosis confirmed by Autism, Diagnostic Interview-Revised (ADI-R).
  • CGI score > = 4 AND an ABC Irritability/Agitation subscale score > = 18 at screening and baseline (randomization)
  • Mental age of at least 18 months
  • Male or female 6 to 17 years of age inclusive, at the time of randomization
Exclusion Criteria
  • Patients considered treatment resistant to neuroleptic medication based on lack of therapeutic response to 2 different neuroleptics after treatment of at least 3 weeks each
  • Patients previously treated and not responding to aripiprazole treatment
  • The patient is currently diagnosed with another disorder on the autism spectrum, including PDD-NOS, Asperger's Disorder, Rett's Disorder, Fragile-X Syndrome or Childhood Disintegrative Disorder
  • Current diagnosis of bipolar disorder, psychosis, schizophrenia, or major depression
  • A seizure in the past year
  • History of severe head trauma or stroke
  • Non-pharmacologic therapy (e.g., psychotherapy, behavior modification) should be stable prior to screening and consistent throughout the study

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
A1Aripiprazole5 mg
A2Aripiprazole10 mg
A3Aripiprazole15 mg
B1Placebo-
Primary Outcome Measures
NameTimeMethod
Mean Change (Week 8 - Baseline) in the Autistic Behavior Checklist (ABC) Irritability Subscale ScoreWeek 8

The ABC is a 58-item informant-based assessment of problem behaviors in children/adolescents with mental retardation. Items are rated on a 4-point scale (0=no problem, 3=severe problem), and resolve into 5 domain subscales. A decrease in score indicates improvement.

Secondary Outcome Measures
NameTimeMethod
Mean Clinical Global Impressions Improvement Scale (CGI-I) ScoreWeek 8

The CGI scale is a clinician-rated global assessment of a patient's improvement over time. Baseline assessment rated a patient's condition on a 7-point scale (1=no symptoms, 7=very severe symptoms). Subsequent assessed improvement relative to baseline symptoms on a 7-point CGI-I item scale (1=very much improved, 7=very much worse).

Number of Participants With Response at Week 8Week 8

Response defined as a ≥ 25% reduction from baseline to endpoint in the ABC Irritability Subscale score and a CGI-I score of 1 or 2 at endpoint.

Mean Change (Week 8 - Baseline) in the Children's Yale-Brown Obsessive Compulsive Scale (CY-BOCS; Compulsion Scale Only)Week 8

CY-BOCS=10-item assessment of obsessive-compulsive symptoms in patients \<18 years. 5 items pertaining to compulsions rate symptoms (time spent, interference with functioning, distress, resistance, control) on a 5-point scale (0=no symptoms/minimum severity, 4=extreme symptoms/maximum severity). A decreased in value indicates improvement.

Mean Change (Week 8 - Baseline) in the Other ABC Subscale ScoresWeek 8

Mean change (Week 8 - baseline) in the other ABC subscale scores (lethargy/social withdrawal; stereotypic behavior; hyperactivity/ noncompliance; inappropriate speech). A decrease in value indicates improvement.

Mean Change (Week 8 - Baseline) in CGI-Severity (CGI-S)Week 8

A CGI-S assessment (a 7-point scale to evaluate the severity of symptoms) was performed at baseline (1=no symptoms; 7=very severe symptoms). The patient's improvement relative to the symptoms at baseline on were assessed on a 7-point CGI-I (1=very much improved; 7=very much worse). A decrease in value indicates improvement.

Summary of Safetycontinuously throughout the study

Deaths, Adverse Events (AEs), Serious AEs (SAEs), Treatment-Emergent AEs and AEs leading to discontinuation

Change From Baseline in Body WeightWeek 8

Adjusted mean change (Week 8 - baseline) in body weight

Trial Locations

Locations (31)

Cambridge Health Alliance

🇺🇸

Medford, Massachusetts, United States

Clinical Innovations, Inc.

🇺🇸

Huntington Beach, California, United States

University Of Florida

🇺🇸

Gainesville, Florida, United States

Stanford University School Of Medicine

🇺🇸

Stanford, California, United States

Institute For Behavioral Medicine

🇺🇸

Smyrna, Georgia, United States

Ladders Clinic

🇺🇸

Wellsley, Massachusetts, United States

Regions Hospital

🇺🇸

St. Paul, Minnesota, United States

North Shore - Long Island Jewish Health System

🇺🇸

Bethpage, New York, United States

Seaver And New York Autism Center Of Excellence

🇺🇸

New York, New York, United States

Pacific Institute Of Medical Sciences

🇺🇸

Bothell, Washington, United States

University Of Alabama At Birmingham

🇺🇸

Birmingham, Alabama, United States

University Of South Florida

🇺🇸

Tampa, Florida, United States

Children'S Hospital Of Michigan

🇺🇸

Detroit, Michigan, United States

The Nisonger Center

🇺🇸

Columbus, Ohio, United States

Harmonex Neuroscience

🇺🇸

Dothan, Alabama, United States

Southwest Autism Research And Resource Center

🇺🇸

Phoenix, Arizona, United States

University Of California-Davis Medical Center

🇺🇸

Sacramento, California, United States

University Of Illinois At Chicago

🇺🇸

Chicago, Illinois, United States

Children'S Mercy Hospital

🇺🇸

Kansas City, Missouri, United States

Munroe-Meyer Institute

🇺🇸

Omaha, Nebraska, United States

The Children'S Hospital

🇺🇸

Aurora, Colorado, United States

Marsella, Gregory

🇺🇸

Boca Raton, Florida, United States

Duke Child And Family Study Center

🇺🇸

Durham, North Carolina, United States

Dallas Pediatric Neurology Associates

🇺🇸

Dallas, Texas, United States

Richmond Behavioral Associates

🇺🇸

Staten Island, New York, United States

Mission Hospitals

🇺🇸

Asheville, North Carolina, United States

Cutting Edge Research

🇺🇸

Oklahoma City, Oklahoma, United States

Western Psychiatric Institute And Clinic

🇺🇸

Pittsburgh, Pennsylvania, United States

Bayou City Research, Ltd.

🇺🇸

Houston, Texas, United States

Children'S National Medical Center

🇺🇸

Fairfax, Virginia, United States

Children'S Hospital Of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

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