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A Study to Assess the Effectiveness and Safety of Irinotecan Liposome Injection, 5-fluorouracil/Leucovorin Plus Oxaliplatin in Patients Not Previously Treated for Metastatic Pancreatic Cancer, Compared to Nab-paclitaxel+Gemcitabine Treatment

Registration Number
NCT04083235
Lead Sponsor
Ipsen
Brief Summary

The purpose of this study is to look at the efficacy and safety of Irinotecan liposome injection in combination with other approved drugs used for cancer therapy, namely 5 fluorouracil/leucovorin (5FU/LV) plus oxaliplatin compared to nab-paclitaxel + gemcitabine treatment in improving the overall survival of patients not previously treated for metastatic pancreatic cancer.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
770
Inclusion Criteria
  • Histological or cytologically confirmed adenocarcinoma of the pancreas that has not been previously treated in the metastatic setting.
  • Initial diagnosis of metastatic disease must have occurred ≤6 weeks prior to screening.
  • Subject has one or more metastatic lesions measurable by computed tomography (CT) scan (or magnetic resonance imaging (MRI), if the subject is allergic to CT contrast media) according to RECIST Version 1.1 criteria.
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.
  • Subject has adequate biological parameters as demonstrated by the following blood counts:(a) Absolute neutrophil count (ANC) ≥2000/mm3 without the use of hemopoietic growth factors within the last 7 days prior to randomisation (b) Platelet count ≥100,000/mm3 (c) Haemoglobin (Hgb) ≥9 g/dL obtained ≤14 days prior to randomisation.
  • Adequate hepatic function as evidenced by: (a) Serum total bilirubin ≤1.5x ULN (biliary drainage is allowed for biliary obstruction), and (b) Aspartate aminotransferase (AST) and alanine aminotransferase (ALT) ≤2.5x upper limit of normal (ULN) (≤5x ULN is acceptable if liver metastases are present).
  • Adequate renal function as evidenced by creatinine clearance ≥30 mL/min.
  • Adequate coagulation studies (obtained ≤14 days prior to randomisation) as demonstrated by prothrombin time and partial thromboplastin time within normal limits (≤1.5xULN ).
Exclusion Criteria
  • Prior treatment of pancreatic cancer in the metastatic setting with surgery, radiotherapy, chemotherapy or investigational therapy
  • Prior treatment of pancreatic adenocarcinoma with chemotherapy in the adjuvant setting, except those where at least 12 months have elapsed since completion of the last dose and no persistent treatment-related toxicities are present.
  • Subject has only localised advanced disease.
  • Documented serum albumin <3 g/dL
  • Known history of central nervous system (CNS) metastases.
  • Clinically significant gastrointestinal disorder
  • History of any second malignancy in the last 2 years
  • Concurrent illnesses that would be a relative contraindication to trial participation
  • Use of strong inhibitors or inducers of CYP3A, CYP2C8 and UGT1A1
  • Neuroendocrine (carcinoid, islet cell) or acinar pancreatic carcinoma
  • Known low or absent dihydropyrimidine dehydrogenase (DPD) activity

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Irinotecan liposome injection + Oxaliplatin + 5-FU/LVIrinotecan Liposomal InjectionIrinotecan liposome injection, oxaliplatin, 5 FU/LV, will be administered on Days 1 and 15 of each 28-day cycle (until progression or unacceptable toxicity).
Irinotecan liposome injection + Oxaliplatin + 5-FU/LV5FluorouracilIrinotecan liposome injection, oxaliplatin, 5 FU/LV, will be administered on Days 1 and 15 of each 28-day cycle (until progression or unacceptable toxicity).
Irinotecan liposome injection + Oxaliplatin + 5-FU/LVLeucovorinIrinotecan liposome injection, oxaliplatin, 5 FU/LV, will be administered on Days 1 and 15 of each 28-day cycle (until progression or unacceptable toxicity).
Nab-paclitaxel + GemcitabineNab-paclitaxelNab-paclitaxel and gemcitabine will be administered on Days 1, 8 and 15 of each 28-day cycle (until progression or unacceptable toxicity).
Irinotecan liposome injection + Oxaliplatin + 5-FU/LVOxaliplatinIrinotecan liposome injection, oxaliplatin, 5 FU/LV, will be administered on Days 1 and 15 of each 28-day cycle (until progression or unacceptable toxicity).
Nab-paclitaxel + GemcitabineGemcitabineNab-paclitaxel and gemcitabine will be administered on Days 1, 8 and 15 of each 28-day cycle (until progression or unacceptable toxicity).
Primary Outcome Measures
NameTimeMethod
Overall Survival (OS)Assessments performed at baseline (within 28 days before start of study treatment), every 8 weeks after first dose, end of treatment (EoT) visit, then every 2 months thereafter up to DCO date of 23 July 2022 (maximum of 893 days)

The OS was defined as time from the date of randomization to the date of death due to any cause. Participants who did not have a date of death recorded at the time of the final analysis were censored at the last known time that the participant was alive. The median OS was measured using Kaplan-Meier technique.

Secondary Outcome Measures
NameTimeMethod
Progression Free Survival (PFS)Assessments performed at baseline (within 28 days before start of study treatment), every 8 weeks after first dose until EoT visit (maximum of 893 days)

PFS was defined as the time from the date of randomization to the first documented disease progression using response evaluation criteria in solid tumors (RECIST) Version 1.1 as per Investigator assessment or death due to any cause. The median PFS was measured using Kaplan-Meier technique.

Overall Response Rate (ORR)Assessments performed at baseline (within 28 days before start of study treatment), every 8 weeks after first dose until EoT visit, (maximum of 893 days)

The ORR was defined as the percentage of participants with a best overall response (BOR) characterized as either a complete response (CR) or partial response (PR) per RECIST Version 1.1. BOR was defined as the best response as recorded from randomization until documented objective disease progression using RECIST Version 1.1. As per RECIST version 1.1, CR is disappearance of all target lesions; PR is \>=30% decrease in the sum of the longest diameter of target lesions; and overall response = CR + PR. The ORR was calculated using Clopper-Pearson method.

Trial Locations

Locations (199)

Oncology Consultants

🇺🇸

Houston, Texas, United States

Miami Cancer Institute

🇺🇸

Miami, Florida, United States

University of Oklahoma - Health Sciences Center

🇺🇸

Oklahoma City, Oklahoma, United States

Mayo Clinic - Scottsdale

🇺🇸

Phoenix, Arizona, United States

Henry Ford Health System

🇺🇸

Detroit, Michigan, United States

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

Kaiser Permanente - Northwest

🇺🇸

Portland, Oregon, United States

Mayo Clinic - Rochester

🇺🇸

Rochester, Minnesota, United States

Instituto Nacional Do Cancer (INCA)

🇧🇷

Rio de Janeiro, Brazil

Alberta Health Services Cross Cancer Institute

🇨🇦

Edmonton, Canada

Oncology Hematology West P.C. dba Nebraska Cancer Specialists

🇺🇸

Omaha, Nebraska, United States

Fundacion Jimenez Diaz

🇪🇸

Madrid, Spain

Hospital Universitario 12 de Octubre

🇪🇸

Madrid, Spain

Florida Cancer Specialists - Fort Myers

🇺🇸

Sarasota, Florida, United States

Florida Cancer Specialists - Panhandle

🇺🇸

Tallahassee, Florida, United States

Rush University Medical Center

🇺🇸

Chicago, Illinois, United States

Edward Hospital - Elmhurst

🇺🇸

Elmhurst, Illinois, United States

Florida Cancer Specialists - East

🇺🇸

West Palm Beach, Florida, United States

Illinois CancerCare - Peoria

🇺🇸

Peoria, Illinois, United States

Carle Cancer Center

🇺🇸

Urbana, Illinois, United States

University of Kentucky Markey Cancer Center

🇺🇸

Lexington, Kentucky, United States

University of Pittsburgh Medical Center (UPMC) - Hillman Cancer Center

🇺🇸

Pittsburgh, Pennsylvania, United States

The West Cancer Center

🇺🇸

Memphis, Tennessee, United States

Houston Methodist Research Institute

🇺🇸

Houston, Texas, United States

Texas Oncology - Tyler

🇺🇸

Tyler, Texas, United States

Virginia Cancer Specialists

🇺🇸

Fairfax, Virginia, United States

Froedtert Hospital and the Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

Sir Charles Gairdner Hospital

🇦🇺

Nedlands, Australia

Centre Antoine-Lacassagne

🇫🇷

Nice, France

Hopital Saint Louis

🇫🇷

Paris, France

Centre Hospitalier Universitaire de Poitiers - Poitiers University Hospital

🇫🇷

Poitiers Cedex, France

Strasbourg Oncologie Liberale

🇫🇷

Strasbourg, France

Slk-Kliniken

🇩🇪

Heilbronn, Germany

Agios Savvas Anticancer Hospital

🇬🇷

Athens, Greece

Dél-pesti Centrumkórház - Szent László Kórház telephely

🇭🇺

Budapest, Hungary

Semmelweis Egyetem Belgyógyászati és Hematológiai Klinika

🇭🇺

Budapest, Hungary

CHA Bundang Medical Center

🇰🇷

Gyeonggi-do, Korea, Republic of

Seoul St. Mary's Hospital, The Catholic University of Korea

🇰🇷

Seoul, Korea, Republic of

Champalimaud Cancer Center

🇵🇹

Lisbon, Portugal

Hospital General Universitario de Elche

🇪🇸

Alicante, Spain

Hospital Universitario de Badajoz

🇪🇸

Badajoz, Spain

Hospital Germans Trias i Pujol

🇪🇸

Badalona, Spain

Hospital General Universitario Gregorio Marañon

🇪🇸

Madrid, Spain

Sarah Cannon and HCA Research Institute

🇺🇸

Nashville, Tennessee, United States

Hospital Universitario Miguel Servet

🇪🇸

Zaragoza, Spain

Florida Cancer Specialists - St. Petersburg

🇺🇸

Tampa, Florida, United States

Toledo Clinic Cancer Center

🇺🇸

Toledo, Ohio, United States

Fort Wayne Medical Oncology and Hematology

🇺🇸

Fort Wayne, Indiana, United States

The Ohio State University Comprehensive Cancer Center - Arthur G. James Cancer Hospital and Richard J. Solovev Research Institute (OSUCCC - James)

🇺🇸

Columbus, Ohio, United States

Banner Health- MD Anderson Cancer Center

🇺🇸

Gilbert, Arizona, United States

University of California- Irvine Health Cancer Cente

🇺🇸

Costa Mesa, California, United States

Comprehensive Blood And Cancer Center

🇺🇸

Bakersfield, California, United States

City of Hope National Medical Center

🇺🇸

Duarte, California, United States

University of California - Irvine Medical Center

🇺🇸

Orange, California, United States

St. Jude Hospital Yorba Linda dba St. Joseph Heritage Healthcare

🇺🇸

Orange, California, United States

University of California, Los Angeles (UCLA)

🇺🇸

Los Angeles, California, United States

Torrance Memorial Physician Network Cancer Care

🇺🇸

Redondo Beach, California, United States

Sutter Health Sacramento

🇺🇸

Sacramento, California, United States

Presbyterian Intercommunity Hospital (PIH)

🇺🇸

Whittier, California, United States

UC Health Memorial Hospital

🇺🇸

Colorado Springs, Colorado, United States

Mount Sinai Medical Center of Florida, Inc.

🇺🇸

Miami Beach, Florida, United States

Rocky Mountain Cancer Center

🇺🇸

Denver, Colorado, United States

Pikeville Medical Center

🇺🇸

Pikeville, Kentucky, United States

Siouxland Hematology - Oncology Associates, LLP

🇺🇸

Sioux City, Iowa, United States

Hematology Oncology Clinic

🇺🇸

Baton Rouge, Louisiana, United States

Willis-Knighton Cancer Center

🇺🇸

Shreveport, Louisiana, United States

Maine Center for Cancer Medicine

🇺🇸

Scarborough, Maine, United States

Beth Israel Deaconess

🇺🇸

Boston, Massachusetts, United States

Maryland Oncology Hematology

🇺🇸

Silver Spring, Maryland, United States

Cancer and Hematology Centers of Western Michigan

🇺🇸

Grand Rapids, Michigan, United States

Health Partners Institute

🇺🇸

Minneapolis, Minnesota, United States

Frontier Cancer Center

🇺🇸

Billings, Montana, United States

Comprehensive Cancer Centers of Nevada

🇺🇸

Las Vegas, Nevada, United States

Clinical Research Alliance, Inc

🇺🇸

Lake Success, New York, United States

Stony Brook University Medical Center

🇺🇸

Stony Brook, New York, United States

David H. Koch Center for Cancer Care at Memorial Sloan Kettering Cancer Center

🇺🇸

New York, New York, United States

University of Rochester

🇺🇸

Rochester, New York, United States

Messino Cancer Center

🇺🇸

Asheville, North Carolina, United States

Oncology Associates of Oregon

🇺🇸

Eugene, Oregon, United States

Compass Oncology - Rose Quarter Cancer Center

🇺🇸

Portland, Oregon, United States

Greenville Hospital System

🇺🇸

Greenville, South Carolina, United States

Oregon Health & Science University (OHSU)

🇺🇸

Portland, Oregon, United States

Chattanooga Oncology Hematology Care - Tennessee Oncology

🇺🇸

Chattanooga, Tennessee, United States

Texas Oncology - Baylor Charles A. Sammons Cancer Center

🇺🇸

Dallas, Texas, United States

Baylor College of Medicine

🇺🇸

Houston, Texas, United States

MD Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Texas Oncology - Wichita Falls

🇺🇸

Wichita Falls, Texas, United States

Utah Cancer Specialists

🇺🇸

Salt Lake City, Utah, United States

Blue Ridge Cancer Care

🇺🇸

Wytheville, Virginia, United States

Bankstown-Lidcombe Hospital

🇦🇺

Bankstown, Australia

Medizinische Universitaet Graz

🇦🇹

Graz, Austria

Monash Medical Centre

🇦🇺

Clayton, Australia

St John of God Subiaco Hospital

🇦🇺

Subiaco, Australia

Ordensklinikum Linz GmbH Barmherzige Schwestern

🇦🇹

Linz, Austria

Queen Elizabeth Hospital

🇦🇺

Woodville South, Australia

SCRI-CCCIT Gemeinnutzige Gmbh- Gemeinnutzige Salzburger Landeskliniken Betriebsgesmbh

🇦🇹

Salzburg, Austria

Medical University of Vienna

🇦🇹

Vienna, Austria

Onze-Lieve-Vrouwziekenhuis

🇧🇪

Aalst, Belgium

ASBL Grand Hôpital de Charleroi (GHdC), Site Notre Dame

🇧🇪

Charleroi, Belgium

Universitair Ziekenhuis Antwerpen (UZA)

🇧🇪

Edegem, Belgium

Hospital centre Jolimont

🇧🇪

Haine-Saint-Paul, Belgium

University Hospital (UZ) Leuven

🇧🇪

Leuven, Belgium

University Hospital Gent

🇧🇪

Gent, Belgium

University Hospital Mont-Godinne

🇧🇪

Yvoir, Belgium

Fundação Pio XII - Hospital de Câncer de Barretos

🇧🇷

Barretos, Brazil

Centro Regional Integrado de Oncologia (CRIO)

🇧🇷

Ceara, Brazil

Centro de Pesquisas Oncológicas - CEPON

🇧🇷

Florianópolis, Brazil

Hospital de Caridade de Ijui

🇧🇷

Ijuí, Brazil

Instituto de Oncologia do Parana - IOP

🇧🇷

Curitiba, Brazil

Clinica Neoplasias Litoral

🇧🇷

Itajaí, Brazil

Centro de Pesquisas Clinicas de Natal - CPCLIN

🇧🇷

Natal, Brazil

Irmandade da Santa Casa de Misericordia de Porto Alegre

🇧🇷

Porto Alegre, Brazil

Hospital Bruno Born

🇧🇷

Lajeado, Brazil

CIP Centro Integrado de Pesquisas do Hospital de Base

🇧🇷

São José Do Rio Preto, Brazil

Instituto do Cancer do Estado de São Paulo (ICESP)

🇧🇷

São Paulo, Brazil

Centre Hospitalier Universitaire de Sherbrooke

🇨🇦

Sherbrooke, Canada

McGill University Faculty of Medicine - Royal Victoria Hospital

🇨🇦

Montréal, Canada

Hôpital Edouard Herriot

🇫🇷

Lyon, France

Masarykuv onkologicky ustav

🇨🇿

Brno, Czechia

University Hospital Olomouc, Department of Oncology

🇨🇿

Olomouc, Czechia

Fakultni nemocnice Hradec Kralove

🇨🇿

Hradec Králové, Czechia

CHRU de Tours - Hôpital Trousseau

🇫🇷

Chambray-lès-Tours, France

Thomayerova Nemocnice

🇨🇿

Praha, Czechia

Centre Oscar Lambret

🇫🇷

Lille, France

Theagenion Hospital

🇬🇷

Thessaloníki, Greece

Centre Leon Berard

🇫🇷

Lyon, France

Hopital Prive Jean Mermoz

🇫🇷

Lyon, France

Facharztzentrum Eppendorf

🇩🇪

Hamburg, Germany

CHU Bordeaux - Hopital Haut-Leveque

🇫🇷

Pessac, France

Charité - Universitaetsmedizin Berlin

🇩🇪

Berlin, Germany

St. Josef-Hospital

🇩🇪

Bochum, Germany

Klinikum Esslingen GmbH

🇩🇪

Esslingen, Germany

Studiengesellschaft BSF

🇩🇪

Halle, Germany

Krankenhaus Nordwest

🇩🇪

Frankfurt, Germany

Martin Luther Universitat Halle-Wittenberg

🇩🇪

Halle, Germany

Asklepios Klinik Altona

🇩🇪

Hamburg, Germany

Medizinische Hochschule Hannover

🇩🇪

Hannover, Germany

Marienkrankenhaus Hamburg

🇩🇪

Hamburg, Germany

Krankenhaus St. Franziskus - Kliniken Maria Hilf GmbH

🇩🇪

Mönchengladbach, Germany

General Hospital of Athens - Laiko

🇬🇷

Athens, Greece

Universitaetsklinikum Ulm

🇩🇪

Ulm, Germany

National and Kapodistrian University of Athens

🇬🇷

Athens, Greece

Universitaetsklinikum Tuebingen

🇩🇪

Tuebingen, Germany

University General Hospital of Ioannina

🇬🇷

Ioánnina, Greece

Országos Onkológiai Intézet

🇭🇺

Budapest, Hungary

Debreceni Egyetem Klinikai Kozpont

🇭🇺

Debrecen, Hungary

Somogy Megyei Kaposi Mor Oktato Korhaz

🇭🇺

Kaposvár, Hungary

Rambam Health Care Campus

🇮🇱

Haifa, Israel

Soroka Medical Center

🇮🇱

Beer Sheva, Israel

Jász-Nagykun-Szolnok Megyei Hetényi Géza Kórház-Rendelointézet

🇭🇺

Szolnok, Hungary

Policlinico S. Orsola-Malpighi

🇮🇹

Bologna, Italy

AUSL di Piacenza-Ospedale Guglielmo Da Saliceto

🇮🇹

Piacenza, Italy

Istituto Europeo di Oncologia

🇮🇹

Milano, Italy

Istituto Romagnolo per lo Studio dei Tumori Dino Amadori

🇮🇹

Meldola, Italy

Azienda Ospedaliero-Universitaria di Modena

🇮🇹

Modena, Italy

Azienda Ospedaliero Universitaria Pisana

🇮🇹

Pisa, Italy

Azienda Ospedaliera - Universitaria Integrata di Verona - Ospedale Borgo Roma

🇮🇹

Verona, Italy

AOU Ospedali Riuniti di Ancona

🇮🇹

Torrette, Italy

Inje University Haeundae Paik Hospital

🇰🇷

Busan, Korea, Republic of

Hospital de Braga

🇵🇹

Braga, Portugal

National Cancer Center

🇰🇷

Goyang-si, Korea, Republic of

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

Centro Hospitalar Universitario de Lisboa Norte - Hospital de Santa Maria

🇵🇹

Lisboa, Portugal

Unidade Local de Saude Matosinhos E.P.E. Hospital Pedro Hispano

🇵🇹

Senhora da Hora, Portugal

Centro Hospitalar de Vila Nova de Gaia/Espinho EPE

🇵🇹

Vila Nova de Gaia, Portugal

Kursk Regional Clinical Oncology Dispensary

🇷🇺

Kursk, Russian Federation

Evimed LLC

🇷🇺

Chelyabinsk, Russian Federation

Main Military Clinical Hospital named after N.N. Burdenko

🇷🇺

Moscow, Russian Federation

Hospital Quironsalud Barcelona

🇪🇸

Barcelona, Spain

Federal State Budgetary Institution - Russian Scientific Center of Radiology and Surgical Technologies n.a. academician A.M.Granov

🇷🇺

Saint-Petersburg, Russian Federation

Hospital de la Santa Creu i Sant Pau Barcelona

🇪🇸

Barcelona, Spain

Volga District Medical Centre

🇷🇺

Novgorod, Russian Federation

Corporacio Sanitaria Parc Tauli - Hospital de Sabadell

🇪🇸

Barcelona, Spain

Hospital Clinic Barcelona

🇪🇸

Barcelona, Spain

Hospital Vall D Hebron

🇪🇸

Barcelona, Spain

Institut Catala d'Oncologia - L'Hospitalet

🇪🇸

Barcelona, Spain

Complejo Hospitalario de Navarra

🇪🇸

Pamplona, Spain

Hospital Universitario La Paz

🇪🇸

Madrid, Spain

Hospital Regional Universitario de Malaga

🇪🇸

Málaga, Spain

Centro Integral Oncologico Clara Campal

🇪🇸

Madrid, Spain

Guy's and St. Thomas' NHS Foundation Trust

🇬🇧

London, United Kingdom

Royal Marsden Foundation Trust

🇬🇧

London, United Kingdom

Hospital Universitario Marques de Valdecilla

🇪🇸

Santander, Spain

Imperial College Healthcare NHS Trust

🇬🇧

London, United Kingdom

Cancer Research UK - Christie Hospital Foundation NHS Trust - Dept of Medical Oncology

🇬🇧

Manchester, United Kingdom

Nottingham City Hospital

🇬🇧

Nottingham, United Kingdom

Fiona Stanley Hospital

🇦🇺

Murdoch, Australia

The Center for Cancer and Blood Disorders

🇺🇸

Fort Worth, Texas, United States

Korea University Guro Hospital

🇰🇷

Seoul, Korea, Republic of

Instituto COI

🇧🇷

Rio De Janeiro, Brazil

Hospital Alemão Oswaldo Cruz

🇧🇷

São Paulo, Brazil

Instituto Brasileiro de Controle do Cancer - IBCC (Sao Paulo)

🇧🇷

San Paolo, Brazil

Klinikum Mannheim

🇩🇪

Mannheim, Germany

Complejo Hospitalario Universitario de Granada - Hospital Universitario Virgen de las Nieves

🇪🇸

Granada, Spain

Limited Liability Company- Clinica Druzhkovyh

🇷🇺

Kazan, Russian Federation

Research Medical Center

🇺🇸

Kansas City, Missouri, United States

Ochsner Clinic Foundation

🇺🇸

New Orleans, Louisiana, United States

Texas Oncology - Austin

🇺🇸

Austin, Texas, United States

Queen Elizabeth II Health Sciences Centre

🇨🇦

Halifax, Canada

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