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The Effectiveness of GM-CSF in HIV-Positive Patients Who Are Also Receiving Anti-HIV Therapy

Phase 2
Completed
Conditions
HIV Infections
Registration Number
NCT00000850
Lead Sponsor
National Institute of Allergy and Infectious Diseases (NIAID)
Brief Summary

The purpose of this study is to see how HIV-positive patients who are taking anti-HIV drugs and have a viral load (level of HIV in the blood) of 1,500 copies/ml or more respond to GM-CSF (granulocyte-macrophage colony-stimulating factor).

GM-CSF is a medication that is being tested in HIV-positive patients to see if it can improve their immune systems or if it can lower the level of HIV in their blood. GM-CSF is often given to patients with leukemia or patients who have received bone marrow transplants to increase their white blood cells and to improve their immune systems. Doctors believe that GM-CSF can increase CD4 counts in HIV-positive patients, but this study will also look at how GM-CSF affects viral load.

Detailed Description

GM-CSF promotes the differentiation and activation of granulocytes, monocytes, macrophages, and dendritic cells and enhances the function of these cells. The various cellular responses (i.e., division, maturation, activation) are induced when GM-CSF binds to specific receptors expressed on the surface of target cells. At higher doses, such as the dose used in this protocol, GM-CSF may result in a rapid rise in white blood cell count. However, further research is necessary to determine the potential antiviral effect of GM-CSF in a potent ART-treated population. It is hoped that GM-CSF can decrease the extent of ongoing HIV replication via alteration of macrophage activation and chemokine receptor expression and that this effect can result in reduction of the pool of latently infected T cells.

Patients are stratified at study entry according to screening CD4 count (below 200 cells/mm3 versus 200 cells/mm3 or higher) and screening HIV-1 RNA copy number (between 1,500 and 10,000 versus 10,000 copies/ml or higher). Then, patients are randomized to receive GM-CSF or GM-CSF placebo subcutaneously 3 times per week for 16 weeks. All patients remain on their current stable potent ART (not provided by this study). During Step 2, all patients receive open-label study treatment, consisting of current potent ART plus GM-CSF subcutaneously 3 times per week for 32 additional weeks. HIV-1 RNA, CD4 counts, and clinical and safety parameters are monitored for all patients periodically until Week 52. Patients who experience an increase in HIV-1 RNA of greater than 1 log 10 from baseline on 2 consecutive determinations or a greater than 50% decrease in CD4 count from baseline (a drop of at least 50 cells) on 2 consecutive determinations at any time during Step 1 or 2 must discontinue all study treatment. Patients who discontinue study treatment for any reason prior to Week 16 continue following the study visit schedule through Week 16.

Additional laboratory samples are performed on patients participating in the immunology substudy (ACTG A5042s) in order to further evaluate the effects of GM-CSF on immune function.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
108
Inclusion Criteria

Not provided

Read More
Exclusion Criteria

Not provided

Read More

Study & Design

Study Type
INTERVENTIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (39)

UCLA CARE Ctr

🇺🇸

Los Angeles, California, United States

Marin County Specialty Clinic

🇺🇸

San Rafael, California, United States

Rush Presbyterian - Saint Luke's Med Ctr

🇺🇸

Chicago, Illinois, United States

Division of Inf Diseases/ Indiana Univ Hosp

🇺🇸

Indianapolis, Indiana, United States

Beth Israel Deaconess - West Campus

🇺🇸

Boston, Massachusetts, United States

Methodist Hosp of Indiana / Life Care Clinic

🇺🇸

Indianapolis, Indiana, United States

MetroHealth Med Ctr

🇺🇸

Cleveland, Ohio, United States

Kaiser Permanente LAMC

🇺🇸

Los Angeles, California, United States

Santa Clara Valley Med Ctr / AIDS Community Rsch Consortium

🇺🇸

San Jose, California, United States

San Mateo AIDS Program / Stanford Univ

🇺🇸

Stanford, California, United States

Bellevue Hosp / New York Univ Med Ctr

🇺🇸

New York, New York, United States

Aaron Diamond AIDS Rsch Ctr / Rockefeller Univ

🇺🇸

New York, New York, United States

Cornell Univ Med Ctr

🇺🇸

New York, New York, United States

Univ of North Carolina

🇺🇸

Chapel Hill, North Carolina, United States

Columbia Presbyterian Med Ctr

🇺🇸

New York, New York, United States

Case Western Reserve Univ

🇺🇸

Cleveland, Ohio, United States

Ohio State Univ Hosp Clinic

🇺🇸

Columbus, Ohio, United States

Julio Arroyo

🇺🇸

West Columbia, South Carolina, United States

Philadelphia Veterans Administration Med Ctr

🇺🇸

Philadelphia, Pennsylvania, United States

Univ of Texas Galveston

🇺🇸

Galveston, Texas, United States

Univ of Washington

🇺🇸

Seattle, Washington, United States

San Francisco Gen Hosp

🇺🇸

San Francisco, California, United States

Univ of Colorado Health Sciences Ctr

🇺🇸

Denver, Colorado, United States

Univ of California / San Diego Treatment Ctr

🇺🇸

San Diego, California, United States

Univ of Miami School of Medicine

🇺🇸

Miami, Florida, United States

Univ of Hawaii

🇺🇸

Honolulu, Hawaii, United States

St Louis Regional Hosp / St Louis Regional Med Ctr

🇺🇸

Saint Louis, Missouri, United States

Northwestern Univ Med School

🇺🇸

Chicago, Illinois, United States

Indiana Univ Hosp

🇺🇸

Indianapolis, Indiana, United States

Duke Univ Med Ctr

🇺🇸

Durham, North Carolina, United States

Mount Sinai Med Ctr

🇺🇸

New York, New York, United States

Willow Clinic

🇺🇸

Menlo Park, California, United States

Harbor UCLA Med Ctr

🇺🇸

Torrance, California, United States

Cook County Hosp

🇺🇸

Chicago, Illinois, United States

Chelsea Ctr

🇺🇸

New York, New York, United States

Boston Med Ctr

🇺🇸

Boston, Massachusetts, United States

Univ of Pennsylvania at Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

Univ of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

Stanford Univ Med Ctr

🇺🇸

Stanford, California, United States

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